New drug trial aims to slow muscle loss in rare genetic disease

NCT ID NCT06411912

Summary

This study tested an investigational drug called NIDO-361 in men with spinal and bulbar muscular atrophy (SBMA), also known as Kennedy's disease. The goal was to see if the drug is safe and if it can help preserve muscle volume and improve physical function over one year. Fifty-four participants were randomly assigned to receive either the drug or a placebo, and neither they nor the doctors knew which they were getting.

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Contacts and locations

Locations

  • Azienda Ospedale Università di Padova

    Padova, Italy

  • IRCCS Istituto Neurologico Carlo Besta

    Milan, Italy

  • Kyungpook National University Chilgok Hospital

    Daegu, South Korea

  • Rigshospitalet, Klinik for Nerve- og Muskelsygdomme & Copenhagen Neuromuscular Center

    Copenhagen, Denmark

  • University of College London Hospital (UCLH)

    London, United Kingdom

Conditions

Explore the condition pages connected to this study.