New drug challenges standard treatment for rare blood disease
NCT ID NCT04434092
Summary
This study is testing whether a new drug called crovalimab works as well as the current standard treatment (eculizumab) for controlling paroxysmal nocturnal hemoglobinuria (PNH), a rare and serious blood disease. It involves 210 adults with PNH who have never taken this type of medication before. The main goals are to see if patients can avoid blood transfusions and control the destruction of their red blood cells over 25 weeks.
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Contacts and locations
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Locations
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*X*CEPHO - Centro de Estudos e Pesquisas em Hematologia e Oncologia
Santo André, São Paulo, 09060-870, Brazil
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Affiliated Hospital of Nantong University
Nantong, 226001, China
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Amsterdam UMC, Locatie AMC
Amsterdam, 1105 AZ, Netherlands
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Asan Medical Center
Seoul, 05505, South Korea
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Beneficencia Portuguesa de Sao Paulo
São Paulo, 01321-00, Brazil
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Centre Hospitalier Lyon Sud
Pierre-Bnite, Rhone, 69310, France
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Centro Hospitalar do Baixo Vouga E.P.E. - Hospital de Aveiro
Aveiro, 3810-501, Portugal
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Centro Hospitalar do Porto - Hospital de Santo António
Porto, 4099-001, Portugal
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Centro Integrado de Oncologia de Curitiba
Curitiba, Paraná, 80810-050, Brazil
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Chang Gung Medical Foundation - Kaohsiung
Kaohisung, DUMMY_VALUE, Taiwan
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General Hospital of Thessaloniki G. Papanikolaou
Thessaloniki, 570 10, Greece
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Global Trial Research Center S.A. de C.V.
Monterrey, Nuevo León, 64718, Mexico
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Hopital Claude Huriez - CHU Lille
Lille, 59037, France
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Hospital Ampang
Ampang, Selangor, 68000, Malaysia
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Hospital Clinic de Barcelona
Barcelona, 08036, Spain
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Hospital General Universitario Gregorio Marañon
Madrid, 28007, Spain
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Hospital Raja Permaisuri Bainun
Ipoh, Perak, 30450, Malaysia
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Hospital San Pedro de Alcantara
Cáceres, 10003, Spain
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Hospital Universitario Clinico San Carlos
Madrid, 28040, Spain
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Hospital Universitario La Paz
Madrid, 28046, Spain
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Hospital Universitario de Gran Canaria Dr. Negrin
Las Palmas de Gran Canaria, LAS Palmas, 35019, Spain
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Hospital Universitario de Salamanca
Salamanca, 37007, Spain
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Hospital de Basurto
Bilbao, Albacete, 48013, Spain
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Huashan Hospital, Fudan University
Shanghai, 200040, China
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ICO Badalona - Hospital Universitari Germans Trias i Pujol
Badalona, Barcelona, 08916, Spain
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Instituto Nacional de Ciencias Medicas y Nutricion Salvador Zubiran
Mexico City, Mexico CITY (federal District), 14080, Mexico
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Instituto Portugues Oncologia de Lisboa Francisco Gentil EPE
Lisbon, 1099-023, Portugal
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Jiangsu Province Hospital
Nanjing, 210029, China
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King Chulalongkorn Memorial Hospital
Pathum Wan, 10330, Thailand
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Kings College Hospital
London, SE5 9RS, United Kingdom
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MTZ Clinical Research Powered by Pratia
Warsaw, 02-172, Poland
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Maharaj Nakorn Chiang Mai Hospital
Chiang Mai, 50200, Thailand
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Mary Mediatrix Medical Center
Lipa City, 4217, Philippines
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Medical Center OK!Clinic+
Kyiv, KIEV Governorate, 02091, Ukraine
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NTT Medical Center Tokyo
Tokyo, 141-8625, Japan
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Nanfang Hospital, Southern Medical University
Guangzhou, 510515, China
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National Taiwan Universtiy Hospital
Taipei, 100, Taiwan
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National University Hospital
Singapore, 119074, Singapore
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Ondokuz Mayis Univ. Med. Fac.
Samsun, 55139, Turkey (Türkiye)
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Organizacion Medica de Investigacion (OMI)
Ciudad Autonoma Buenos Aires, C1015ABO, Argentina
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Peking Union Medical College Hospital
Beijing, 100730, China
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Philippine General Hospital
Manila, 1000, Philippines
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Pratia Poznan
Skórzewo, 60-185, Poland
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Samodzielny Publiczny Szpital Kliniczny nr 1
Lublin, 20-081, Poland
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Samsung Medical Center
Seoul, 06351, South Korea
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Sapporo Medical University Hospital
Hokkaido, 060-8543, Japan
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Seoul National University Hospital
Seoul, 03080, South Korea
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Severance Hospital, Yonsei University Health System
Seoul, 03722, South Korea
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Singapore General Hospital
Singapore, 169856, Singapore
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Siriraj Hospital
Bangkok, 10700, Thailand
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Spitalul Clinic Municipal Filantropia Craiova
Craiova, 200143, Romania
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Spitalul Universitar de Urgenta Bucuresti
Bucharest, 050098, Romania
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St James University Hospital
Leeds, LS9 7TF, United Kingdom
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St Lukes Medical Center
Quezon, 1102, Philippines
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Szpital Uniwersytecki nr2 im. dr J. Biziela
Bydgoszcz, 85-168, Poland
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The First Affiliated Hospital, Zhejiang University
Hangzhou, 310003, China
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Tokyo Medical University Hospital
Tokyo, 160-0023, Japan
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Union Hospital Tongji Medical College Huazhong University of Science and Technology
Wuhan, 430022, China
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Universitaetsklinikum Ulm
Ulm, 89081, Germany
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Universitaetsklinkm
Essen, 45147, Germany
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University of Tsukuba Hospital
Ibaraki, 305-8576, Japan
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Uniwersyteckie Centrum Kliniczne
Gdansk, 80-952, Poland
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Vilnius University Hospital Santariskiu Clinics, Public Institution
Vilnius, LT-08661, Lithuania
Conditions
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