New drug challenges standard treatment for rare blood disease

NCT ID NCT04432584

Summary

This study is testing whether a new drug called crovalimab works as well as or better than the standard treatment (eculizumab) for controlling paroxysmal nocturnal hemoglobinuria (PNH), a rare blood disorder. It will involve about 190 people who are already being treated for PNH. The main goal is to see if the new drug is safe and effective for long-term disease management.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • *X*CEPHO - Centro de Estudos e Pesquisas em Hematologia e Oncologia

    Santo André, São Paulo, 09060-870, Brazil

  • AZ Delta Campus Westlaan

    Roeselare, 8800, Belgium

  • Akademiska Sjukhuset

    Uppsala, 751 85, Sweden

  • Amsterdam UMC, Locatie AMC

    Amsterdam, 1105 AZ, Netherlands

  • Attikon University General Hospital

    Athens, 124 62, Greece

  • Azienda Ospedaliera Città della Salute e della Scienza di Torino

    Turin, Piedmont, 10126, Italy

  • Azienda Ospedaliera Universitaria Careggi

    Florence, Tuscany, 50134, Italy

  • Azienda Unita Sanitaria Locale- Ravenna

    Ravenna, Emilia-Romagna, 48121, Italy

  • Beneficencia Portuguesa de Sao Paulo

    São Paulo, 01321-00, Brazil

  • CHU UCL Namur / site Godinne

    Yvoir, 5530, Belgium

  • Carolinas Healthcare System

    Charlotte, North Carolina, 28204, United States

  • Centro Hospitalar do Baixo Vouga E.P.E. - Hospital de Aveiro

    Aveiro, 3814-501, Portugal

  • Centro Hospitalar do Porto - Hospital de Santo António

    Porto, 4099-001, Portugal

  • Changhua Christian Hospital

    Chang-hua, 500, Taiwan

  • Chronos Pesquisa Clinica

    Taguatinga, Federal District, 72145-450, Brazil

  • Cliniques Universitaires Saint-Luc

    Brussels, 1200, Belgium

  • Complejo Hospitalario Universitario de Santiago.

    Santiago de Compostela, LA Coruna, 15706, Spain

  • ELBLANDKLINIKUM Riesa

    Riesa, 01589, Germany

  • Ege University Medical Faculty; Hematology

    Izmir, 35040, Turkey (Türkiye)

  • Fondazione IRCCS CA? Granda Ospedale Maggiore Policlinico

    Milan, Lombardy, 20122, Italy

  • Fondazione Policlinico Universitario Agostino Gemelli IRCCS

    Rome, Lazio, 00168, Italy

  • Fujita Health University Hospital

    Aichi, 470-1192, Japan

  • Gaziantep University Medical Faculty Sahinbey Educational Research Hospital; Hematology

    Gaziantep, 27310, Turkey (Türkiye)

  • General Hospital of Athens LAIKO

    Athens, 115 27, Greece

  • Hacettepe University Medical Faculty; Neurology

    Ankara, 06100, Turkey (Türkiye)

  • Hopital Claude Huriez - CHU Lille

    Lille, 59037, France

  • Hospital General Universitario Gregorio Marañon

    Madrid, 28009, Spain

  • Hospital Paulistano

    São Paulo, São Paulo, 01321-000, Brazil

  • Hospital Regional Universitario de Malaga

    Málaga, 29010, Spain

  • Hospital Sírio-Libanês

    São Paulo, São Paulo, 01308-050, Brazil

  • Hospital U. Central de Asturias

    Asturias, Principality of Asturias, 33011, Spain

  • Hospital Universitari Vall d'Hebron

    Barcelona, 08035, Spain

  • Hospital Universitario Clinico San Carlos

    Madrid, 28040, Spain

  • Hospital Universitario Miguel Servet

    Zaragoza, 50009, Spain

  • Hospital Universitario Virgen del Rocio

    Seville, 41013, Spain

  • Hospital Universitario de Salamanca

    Salamanca, 37007, Spain

  • Hospital Universitario de Toledo

    Toledo, 45007, Spain

  • Hospital das Clínicas FMRP-USP

    Ribeirão Preto, São Paulo, 14048-900, Brazil

  • Hospital de Basurto

    Bilbao, Vizcaya, 48013, Spain

  • Hospital de Clínicas de Porto Alegre X

    Porto Alegre, Rio Grande do Sul, 90035-903, Brazil

  • Hualien Tzu Chi Hospital

    Hualien City, DUMMY_VALUE, Taiwan

  • ICO Badalona - Hospital Universitari Germans Trias i Pujol

    Badalona, Barcelona, 08916, Spain

  • Instituto Joinvilense de Hematologia E Oncologia

    Joinville, Santa Catarina, 89201-260, Brazil

  • Ishikawa Prefectural Central Hospital

    Ishikawa, 920-8530, Japan

  • Istanbul University Istanbul Medical Faculty; Neurology

    Istanbul, 34093, Turkey (Türkiye)

  • Iwate Prefectural Isawa Hospital

    Ōshū, 023-0864, Japan

  • Japanese Red Cross Society Suwa Hospital

    Nagano, 392-8510, Japan

  • King Faisal Specialist Hospital & Research Center

    Riyadh, 11211, Saudi Arabia

  • King'S College Hospital

    London, SE5 9RS, United Kingdom

  • Kobe University Hospital

    Hyōgo, 650-0017, Japan

  • MTZ Clinical Research Powered by Pratia

    Warsaw, 02-172, Poland

  • Marmara University Pendik Training and Research Hospital, Hematology Department

    Istanbul, 34300, Turkey (Türkiye)

  • Mie University Hospital

    Mie, 514-8507, Japan

  • NTT Medical Center Tokyo

    Tokyo, 141-8625, Japan

  • Nagasaki University Hospital

    Nagasaki, 852-8501, Japan

  • National Hospital Organization Okayama Medical Center

    Okayama, 701-1192, Japan

  • National Taiwan Universtiy Hospital

    Taipei, 100, Taiwan

  • National University Hospital

    Singapore, 117599, Singapore

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States

  • North Estonia Medical Centre Foundation

    Tallinn, 13419, Estonia

  • Ondokuz Mayis Univ. Med. Fac.

    Samsun, 55139, Turkey (Türkiye)

  • Pratia Poznan

    Skórzewo, 60-185, Poland

  • Prince of Wales Hospital

    Hong Kong, 999077, Hong Kong

  • Samodzielny Publiczny Szpital Kliniczny nr 1

    Lublin, 20-081, Poland

  • Samsung Medical Center

    Seoul, 06351, South Korea

  • Santa Casa de Misericordia de Porto Alegre

    Porto Alegre, Rio Grande do Sul, 90020-090, Brazil

  • Sasebo City General Hospital

    Nagasaki, 857-8511, Japan

  • Semmelweis Egyetem

    Budapest, 1088, Hungary

  • Seoul National University Hospital

    Seoul, 03080, South Korea

  • Severance Hospital

    Seoul, 03722, South Korea

  • St James's Hospital

    Dublin, D08NYH1, Ireland

  • Szpital Uniwersytecki nr2 im. dr J. Biziela

    Bydgoszcz, 85-168, Poland

  • The University of Osaka Hospital

    Osaka, 565-0871, Japan

  • Tokai University Hospital

    Kanagawa, 259-1193, Japan

  • Tokushukai Takasago Seibu Hospital

    Hyōgo, 676-0812, Japan

  • Tokyo Medical University Hospital

    Tokyo, 160-0023, Japan

  • Toyama Prefectual Central Hospital

    Toyama, 930-8550, Japan

  • Ulsan University Hospital

    Ulsan, 44033, South Korea

  • Universitaetsklinikum Aachen AOeR

    Aachen, 52074, Germany

  • Uniwersyteckie Centrum Kliniczne

    Gda?sk, 80-214, Poland

  • Ustav hematologie a krevni transfuze

    Prague, 128 00, Czechia

Conditions

Explore the condition pages connected to this study.