Rare disease mystery unraveled: 5-Year study tracks atypical morquio a

NCT ID NCT03204370

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study followed 7 adults with a milder form of Morquio A disease for 5 years to learn how the condition changes over time. Researchers measured walking ability and other health factors to better understand the disease and improve future treatment evaluations. The goal was to gather knowledge, not to test a new treatment.

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Conditions

The condition(s) this trial relates to.

Mucopolysaccharidosis IV mucopolysaccharidosis type 4A

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Rheumatology department - Bordeaux University Hospital

    Bordeaux, Aquitaine, 33076, France

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Other studies related to the condition(s) this trial covers.