Last-Resort drug opens door for transplant patients with rare blood clotting complication

NCT ID NCT04247906

First seen Jan 03, 2026 · Last updated May 15, 2026 · Updated 25 times

Summary

This program gives patients who have had a stem cell transplant and developed a serious blood clotting condition (HSCT-TMA) access to an experimental drug called narsoplimab. The goal is to control the disease when no other options are available. Adults and children who meet the criteria can receive treatment based on their doctor's judgment.

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