Massive study launched to map rare disease journey

NCT ID NCT06036693

Summary

This study aims to gather detailed health information from 1000 French patients with a group of rare genetic disorders called Mucopolysaccharidosis (MPS). Researchers will look back at past medical records and follow patients forward to understand how these diseases naturally progress and how different treatments affect them. The goal is to build a comprehensive picture to help improve future care.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • American Memorial Hospital

    NOT_YET_RECRUITING

    Reims, France

    Contact

  • Centre Hospitalier Universitaire d'Angers

    RECRUITING

    Angers, France

    Contact

  • Centre Hospitalier de Pau

    RECRUITING

    Pau, France

    Contact

  • Clinique Monié

    NOT_YET_RECRUITING

    Toulouse, France

    Contact

  • Hôpital Armand Trousseau

    RECRUITING

    Paris, France

    Contact

  • Hôpital Beaujon

    RECRUITING

    Clichy, France

    Contact

  • Hôpital Brabois

    RECRUITING

    Nancy, France

    Contact

  • Hôpital Charles Nicolle

    NOT_YET_RECRUITING

    Rouen, France

    Contact

  • Hôpital Clocheville

    RECRUITING

    Tours, France

    Contact

  • Hôpital Gui de Chauliac

    RECRUITING

    Montpellier, France

    Contact

  • Hôpital Jeanne de Flandre

    RECRUITING

    Lille, France

    Contact

  • Hôpital Morvan

    RECRUITING

    Brest, France

    Contact

  • Hôpital Necker-Enfants Malades

    RECRUITING

    Paris, France

    Contact

  • Hôpital Pontchaillou

    RECRUITING

    Rennes, France

    Contact

  • Hôpital Raymond-Poincaré

    NOT_YET_RECRUITING

    Garches, France

    Contact

  • Hôpital Robert Debré

    RECRUITING

    Paris, France

    Contact

  • Hôpital d'Estaing

    NOT_YET_RECRUITING

    Clermont-Ferrand, France

    Contact

  • Hôpital de Hautepierre

    NOT_YET_RECRUITING

    Strasbourg, France

    Contact

  • Hôpital de la Croix Saint-Simon

    NOT_YET_RECRUITING

    Paris, France

    Contact

  • Hôpital de la Pitié-Salpêtrière

    RECRUITING

    Paris, France

    Contact

  • Hôpital de la Timone

    RECRUITING

    Marseille, France

    Contact

  • Hôpital des Enfants

    NOT_YET_RECRUITING

    Toulouse, France

    Contact

  • Hôpital des Enfants - Groupe Hospitalier Pellegrin

    NOT_YET_RECRUITING

    Bordeaux, France

    Contact

Conditions

Explore the condition pages connected to this study.