Hope for rare overgrowth disease: first treatment trial
NCT ID NCT04316546
Summary
This study is testing whether a drug called miransertib can safely slow or stop the abnormal tissue overgrowth caused by Proteus syndrome, a rare and serious genetic condition. It will involve about 45 participants aged 3 and older who have a confirmed diagnosis. Participants will take a daily pill for up to 4 years while researchers monitor changes in their condition, pain levels, and quality of life.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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National Institutes of Health Clinical Center
RECRUITINGBethesda, Maryland, 20892, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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