New combo therapy holds promise for kids with rare leukemia

NCT ID NCT03591510

First seen Nov 01, 2025 · Last updated May 13, 2026 · Updated 26 times

Summary

This study tests whether adding the drug midostaurin to standard chemotherapy can safely control a rare, aggressive leukemia (FLT3-mutated AML) in children. About 22 children will receive the drug twice daily alongside chemo, then continue midostaurin alone for 12 more cycles. The goal is to manage the disease, not cure it, since ongoing treatment may be needed.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Novartis Investigative Site

    Prague, 150 06, Czechia

  • Novartis Investigative Site

    Berlin, 13353, Germany

  • Novartis Investigative Site

    Essen, 45147, Germany

  • Novartis Investigative Site

    Pavia, PV, 27100, Italy

  • Novartis Investigative Site

    Roma, RM, 00165, Italy

  • Novartis Investigative Site

    Torino, TO, 10126, Italy

  • Novartis Investigative Site

    Naples, 80122, Italy

  • Novartis Investigative Site

    Osaka, 5340021, Japan

  • Novartis Investigative Site

    Amman, 11941, Jordan

  • Novartis Investigative Site

    Krakow, 30-663, Poland

  • Novartis Investigative Site

    Moscow, 117198, Russia

  • Novartis Investigative Site

    Ljubljana, 1000, Slovenia

  • Novartis Investigative Site

    Seoul, 03080, South Korea

  • Novartis Investigative Site

    Seoul, 05505, South Korea

  • Novartis Investigative Site

    Adana, Adana, 1330, Turkey (Türkiye)

Conditions

Explore the condition pages connected to this study.