Hope for tots with rare fat disorder: trial tests lifesaving drug
NCT ID NCT06502990
Summary
This study is testing a drug called metreleptin in children under 6 years old who have a rare condition called generalized lipodystrophy, which causes severe problems with fat storage, diabetes, and high blood fats. The main goal is to see if the drug safely lowers blood sugar and triglyceride levels over 12 months. It aims to help manage this serious lifelong condition in very young patients.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Assistance Publique-Hopitaux de Paris (AP-HP) - Hopital Universitaire Robert-Debre
RECRUITINGParis, France
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Azienda Ospedaliera Universitaria "Federico II"
RECRUITINGNaples, 80131, Italy
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Azienda Ospedaliero Universitaria Maggiore della Carità di Novara
RECRUITINGNovara, 28100, Italy
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Azienda Ospedaliero Universitaria Pisana
RECRUITINGPisa, 56124, Italy
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Azienda Ospedaliero-Universitaria di Parma
RECRUITINGParma, 43126, Italy
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Hôpital Necker - Enfants Malades
RECRUITINGParis, 75015, France
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IRCCS Ospedale Pediatrico Bambino Gesù
RECRUITINGChieti, 66100, Italy
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IRCCS Ospedale Pediatrico Bambino Gesù
RECRUITINGRome, 00165, Italy
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Ospedale Filippo Del Ponte Varese - ASST Sette Laghi
RECRUITINGVarese, 21100, Italy
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UZ Leuven
RECRUITINGLeuven, 3000, Belgium
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Universitaetsklinikum Ulm - Klinik fuer Kinder- und Jugendmedizin
RECRUITINGUlm, 89075, Germany
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Universitätsklinikum Hamburg-Eppendorf
NOT_YET_RECRUITINGHamburg, 20251, Germany
Contact
Conditions
Explore the condition pages connected to this study.