Hope for tots with rare fat disorder: trial tests lifesaving drug

NCT ID NCT06502990

Summary

This study is testing a drug called metreleptin in children under 6 years old who have a rare condition called generalized lipodystrophy, which causes severe problems with fat storage, diabetes, and high blood fats. The main goal is to see if the drug safely lowers blood sugar and triglyceride levels over 12 months. It aims to help manage this serious lifelong condition in very young patients.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Assistance Publique-Hopitaux de Paris (AP-HP) - Hopital Universitaire Robert-Debre

    RECRUITING

    Paris, France

    Contact

  • Azienda Ospedaliera Universitaria "Federico II"

    RECRUITING

    Naples, 80131, Italy

    Contact

  • Azienda Ospedaliero Universitaria Maggiore della Carità di Novara

    RECRUITING

    Novara, 28100, Italy

    Contact

  • Azienda Ospedaliero Universitaria Pisana

    RECRUITING

    Pisa, 56124, Italy

    Contact

  • Azienda Ospedaliero-Universitaria di Parma

    RECRUITING

    Parma, 43126, Italy

    Contact

  • Hôpital Necker - Enfants Malades

    RECRUITING

    Paris, 75015, France

    Contact

  • IRCCS Ospedale Pediatrico Bambino Gesù

    RECRUITING

    Chieti, 66100, Italy

    Contact

  • IRCCS Ospedale Pediatrico Bambino Gesù

    RECRUITING

    Rome, 00165, Italy

    Contact

  • Ospedale Filippo Del Ponte Varese - ASST Sette Laghi

    RECRUITING

    Varese, 21100, Italy

    Contact

  • UZ Leuven

    RECRUITING

    Leuven, 3000, Belgium

    Contact

  • Universitaetsklinikum Ulm - Klinik fuer Kinder- und Jugendmedizin

    RECRUITING

    Ulm, 89075, Germany

    Contact

  • Universitätsklinikum Hamburg-Eppendorf

    NOT_YET_RECRUITING

    Hamburg, 20251, Germany

    Contact

Conditions

Explore the condition pages connected to this study.