Registry launched to track Real-World effects of rare disease drug
NCT ID NCT02325674
Summary
This study is creating a registry to monitor patients who are already taking the drug metreleptin for lipodystrophy, a rare disorder affecting body fat. The goal is to collect long-term safety information on side effects and how well the treatment works in everyday medical practice, outside of controlled clinical trials. It will track up to 100 patients in the US and Europe who are receiving the drug commercially.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Addenbrooke's Hospital
RECRUITINGCambridge, CB2 0QQ, United Kingdom
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Alma Mater Studiorum - Università di Bologna
RECRUITINGBologna, 40126, Italy
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Ann & Robert H. Lurie Children's Hospital of Chicago
RECRUITINGChicago, Illinois, 60611, United States
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Atlanta Diabetes Associates
ACTIVE_NOT_RECRUITINGAtlanta, Georgia, 30318, United States
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Azienda Ospedaliera Universitaria Policlinico Tor Vergata
WITHDRAWNRoma, 00133, Italy
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Azienda Ospedaliero Universitaria Pisana (Presidio di Cisanello)
RECRUITINGPisa, 56124, Italy
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CHRU Hôpital Claude Huriez
RECRUITINGLille, Nord, 59800, France
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Children's Hospital of New Orleans/LSU Health Sciences Center
COMPLETEDNew Orleans, Louisiana, 70118, United States
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Children's Hospital of Philadelphia
RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
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Childrens Hospital of Michigan
RECRUITINGDetroit, Michigan, 48201, United States
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City of Hope
TERMINATEDDuarte, California, 91010, United States
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Endocrinology Research Associates
RECRUITINGColumbus, Ohio, 43201, United States
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Hôpital Robert Debré
RECRUITINGParis, Paris, France, 75019, France
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Hôpital Saint-Antoine
RECRUITINGParis, 75012, France
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Kinderkrankenhaus Auf der Bult
RECRUITINGHanover, Lower Saxony, 0000, Germany
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Nih/Niddk/Deob
RECRUITINGBethesda, Maryland, 20892, United States
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Ochsner Clinic Foundation
WITHDRAWNNew Orleans, Louisiana, 70121, United States
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Richmond University Medical Centre
COMPLETEDStaten Island, New York, 10314, United States
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Seattle Children's Hospital
RECRUITINGSeattle, Washington, 98105, United States
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UT Southwestern Medical Center
RECRUITINGDallas, Texas, 75390, United States
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Universita del Piemonte Orientale "Amedeo Avogadro"
RECRUITINGNovara, Verceilli, 13100, Italy
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Universitaetsklinikum Leipzig AoeR
RECRUITINGLeipzig, Saxony, 04103, Germany
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Universitaetsklinikum Muenster
RECRUITINGMünster, North Rhine-Westphalia, 48149, Germany
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Universitaetsklinikum Ulm
RECRUITINGUlm, Baden-Wurttemberg, 89075, Germany
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University Alabama at Birmingham
TERMINATEDBirmingham, Alabama, 40506, United States
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University of Kansas Medical Center Research Institute, Inc.
RECRUITINGKansas City, Kansas, 66160, United States
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University of Michigan
RECRUITINGAnn Arbor, Michigan, 48109, United States
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University of Pennsylvania
WITHDRAWNPhiladelphia, Pennsylvania, 19104, United States
Conditions
Explore the condition pages connected to this study.