New hope for toddlers with rare fat-loss disease as drug trial begins
NCT ID NCT06502990
First seen Jan 22, 2026 · Last updated May 16, 2026 · Updated 20 times
Summary
This study tests a drug called metreleptin in children under 6 who have generalized lipodystrophy, a rare condition where the body loses fat tissue, leading to severe diabetes and high blood fats. The goal is to see if the drug safely lowers blood sugar and fat levels. About 15 children who have not taken metreleptin before will join this open-label trial.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Assistance Publique-Hopitaux de Paris (AP-HP) - Hopital Universitaire Robert-Debre
RECRUITINGParis, France
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Azienda Ospedaliera Universitaria "Federico II"
RECRUITINGNaples, 80131, Italy
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Azienda Ospedaliero Universitaria Maggiore della Carità di Novara
RECRUITINGNovara, 28100, Italy
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Azienda Ospedaliero Universitaria Pisana
RECRUITINGPisa, 56124, Italy
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Azienda Ospedaliero-Universitaria di Parma
RECRUITINGParma, 43126, Italy
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Hôpital Necker - Enfants Malades
RECRUITINGParis, 75015, France
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IRCCS Ospedale Pediatrico Bambino Gesù
RECRUITINGChieti, 66100, Italy
Contact
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IRCCS Ospedale Pediatrico Bambino Gesù
RECRUITINGRome, 00165, Italy
Contact
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Ospedale Filippo Del Ponte Varese - ASST Sette Laghi
RECRUITINGVarese, 21100, Italy
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UZ Leuven
RECRUITINGLeuven, 3000, Belgium
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Universitaetsklinikum Ulm - Klinik fuer Kinder- und Jugendmedizin
RECRUITINGUlm, 89075, Germany
Contact
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Universitätsklinikum Hamburg-Eppendorf
NOT_YET_RECRUITINGHamburg, 20251, Germany
Contact
Conditions
Explore the condition pages connected to this study.