New hope for rare liver itch: phase 3 drug trial underway

NCT ID NCT06553768

First seen Jan 10, 2026 · Last updated May 16, 2026 · Updated 22 times

Summary

This study tests a drug called maralixibat for people with rare liver diseases who suffer from severe itching that hasn't responded to other treatments. About 90 children and adults will receive either the drug or a placebo to see if it safely reduces itching. The goal is to improve quality of life for those with no other options.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Azienda Ospedaliera Papa Giovanni XXIII

    Bergamo, 24127, Italy

  • Baylor College of Medicine

    Houston, Texas, 77030, United States

  • Children's Hospital Los Angeles (CHLA)

    Los Angeles, California, 90027, United States

  • Cincinnati Children's Hospital Medical Center

    Cincinnati, Ohio, 45229, United States

  • Hospital Sírio-Libanês

    São Paulo, Brazil

  • Hospital Universitario La Paz

    Madrid, Spain

  • Hospital Universitario Vall d'Hebron

    Barcelona, Spain

  • Hospital da Criança Santo Antonio

    Porto Alegre, Brazil

  • Hospital de Criança de Brasília (HCB)

    Brasília, Brazil

  • Hotel Dieu de France

    Beirut, Lebanon

  • Hôpital Kremlin Bicêtre

    Paris, France

  • Hôpitaux Universitaires de Marseille Timone

    Marseille, 13005, France

  • ISMETT - Istituto Mediterraneo per i Trapianti e Terapie ad Alta Specializzazione

    Palermo, 90127, Italy

  • Instytut Pomnik Centrum Zdrowia Dziecka

    Warsaw, Poland

  • King's College Hospital NHS Foundation Trust

    London, United Kingdom

  • Lurie Children's Hospital

    Chicago, Illinois, 60611, United States

  • Morgan Stanley Children's Hospital - NewYork Presbyterian

    New York, New York, 10032, United States

  • Mount Sinai Hospital

    New York, New York, 10029, United States

  • NYU Langone Health

    New York, New York, 10016, United States

  • Ospedale Pediatrico Bambino Gesu

    Rome, 00165, Italy

  • Stanford Children's Health in Palo Alto

    Palo Alto, California, 94304, United States

  • Stollery Children's Hospital

    Edmonton, Alberta, T6G 2B7, Canada

  • University of Utah

    Salt Lake City, Utah, 84112, United States

  • Universitätsklinikum Hamburg Eppendorf - Klinik für Kinder- und Jugendmedizin

    Hamburg, Germany

Conditions

Explore the condition pages connected to this study.