New drug trial offers hope for kids with blood disorder

NCT ID NCT04143724

Summary

This study is testing a drug called luspatercept in children aged 6 to 18 with beta-thalassemia, a genetic blood disorder. Researchers want to find the safest dose and see how the drug affects the body, with the goal of reducing the need for blood transfusions and improving hemoglobin levels. Children who benefit from the treatment can continue taking it for up to 5 years.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

Locations

  • AOU dell'Universita degli Studi della Campania Luigi Vanvitelli

    RECRUITING

    Naples, 80131, Italy

    Contact Phone: •••-•••-••••

  • Azienda Ospedaliero Universitaria S. Luigi Gonzaga

    RECRUITING

    Orbassano, 10043, Italy

    Contact

  • Christian Medical College & Hospital

    RECRUITING

    Vellore, 632004, India

    Contact

  • Chulalongkorn University Faculty of Medicine - King Chulalongkorn Memorial Hospital

    RECRUITING

    Bangkok, 10330, Thailand

    Contact

  • Ente Ospedaliero Ospedali Galliera - Centro della Microcitemia e delle Anemie Congenite

    RECRUITING

    Genoa, 16128, Italy

    Contact Phone: •••-•••-••••

  • General Children's Hospital "Agia Sophia"

    RECRUITING

    Athens, 115 27, Greece

    Contact Phone: •••-•••-••••

  • Kamala Hospital and Research Center

    RECRUITING

    Hyderabad, Andhra Pradesh, 500052, India

    Contact

  • Kingsway Hospitals

    RECRUITING

    Nagpur, Maharashtra, 440001, India

    Contact

  • Local Institution - 401

    COMPLETED

    Izmir, 35100, Turkey (Türkiye)

  • Local Institution - 601

    COMPLETED

    Los Angeles, California, 90027, United States

  • Local Institution - 700

    WITHDRAWN

    Beirut, 0, Lebanon

  • Local Institution - 803

    WITHDRAWN

    Kolkata, 700094, India

  • MCGM - Comprehensive Thalassemia Care, Pediatric Hematology-Oncology & BMT Centre, Borivali (E)

    RECRUITING

    Mumbai, Maharashtra, 400022, India

    Contact

  • New York Presbyterian Hospital

    RECRUITING

    New York, New York, 10065-4870, United States

    Contact Phone: •••-•••-••••

  • Ospedale Pediatrico Bambino Gesù IRCCS

    RECRUITING

    Rome, Roma, 00165, Italy

    Contact Phone: •••-•••-••••

  • People's Liberation Army The 923rd Hospital

    RECRUITING

    Nanning, GX, 530021, China

    Contact Phone: •••-•••-••••

  • Post Graduate Institute of Child Health

    RECRUITING

    Noida, Uttar Pradesh, 201303, India

    Contact Phone: •••-•••-••••

  • Ramathibodi Hospital, Mahidol University

    RECRUITING

    Phyathai, 10400, Thailand

    Contact

  • Shenzhen Second People's Hospital

    RECRUITING

    Shenzhen, Guangdong, 518028, China

    Contact Phone: •••-•••-••••

  • Siriraj Hospital Mahidol University

    RECRUITING

    Bangkok, 10700, Thailand

    Contact Phone: •••-•••-••••

  • Southern Medical University Nanfang Hospital

    RECRUITING

    Guangzhou, Guangdong, 510515, China

    Contact

  • Sun Yat-sen Memorial Hospital, Sun Yat-Sen University

    RECRUITING

    Guangzhou, 510120, China

    Contact Phone: •••-•••-••••

  • The First Affiliated Hospital of Guangxi Medical University

    RECRUITING

    Nanning, 530021, China

    Contact Phone: •••-•••-••••

  • Universitatsklinikum Ulm

    RECRUITING

    Ulm, 89081, Germany

    Contact Phone: •••-•••-••••

  • Universitätsklinikum Essen

    RECRUITING

    Essen, 45147, Germany

    Contact

  • West China Hospital - Sichuan University

    RECRUITING

    Chengdu, Sichuan, 610041, China

    Contact

Conditions

Explore the condition pages connected to this study.