New pill shows promise against childhood cancer that Won't quit

NCT ID NCT03107988

First seen Nov 01, 2025 · Last updated May 16, 2026 · Updated 28 times

Summary

This study tested a new daily pill called lorlatinib in 65 children and young adults with a type of nerve cancer (neuroblastoma) that had come back or not responded to treatment. The drug targets a specific genetic change in the cancer cells. The main goals were to find the safest dose and understand side effects, both when given alone and with chemotherapy.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • C.S Mott Children's Hospital

    Ann Arbor, Michigan, 48109, United States

  • Children Hospital of Colorado

    Aurora, Colorado, 80045, United States

  • Children's Healthcare of Atlanta

    Atlanta, Georgia, 30322, United States

  • Children's Hospital Los Angeles

    Los Angeles, California, 90027-0700, United States

  • Children's Hospital and Regional Medical Center - Seattle

    Seattle, Washington, 98105, United States

  • Children's Hospital of Philadelphia

    Philadelphia, Pennsylvania, 19104-4318, United States

  • Childrens Hospital Boston, Dana-Farber Cancer Institute.

    Boston, Massachusetts, 02115, United States

  • Cook Children's Healthcare System

    Fort Worth, Texas, 76104, United States

  • Hospital for Sick Children

    Toronto, Ontario, M5G 1X8, Canada

  • Institut Curie

    Paris, Cedex, 05, France

  • Royal Marsden Hospital

    Sutton, Surrey, SM25NG, United Kingdom

  • UCSF Helen Diller Family Comprehensive Cancer Center

    San Francisco, California, 94143, United States

  • University of Chicago, Comer Children's Hospital

    Chicago, Illinois, 60637, United States

Conditions

Explore the condition pages connected to this study.