New study tracks Real-World safety of hATTR-PN drug TEGSEDI

NCT ID NCT04850105

First seen Sep 30, 2025 · Last updated May 02, 2026 · Updated 25 times

Summary

This study follows 240 adults with hereditary transthyretin amyloidosis with polyneuropathy (hATTR-PN) to monitor the long-term safety of the drug TEGSEDI. Researchers will compare patients who have taken TEGSEDI with those who have not, focusing on risks like low platelet counts. The goal is to better understand the drug's safety in everyday medical practice.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Study Center

    RECRUITING

    Lille, Cedex, 59037, France

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    Nice, Romaine, 06001, France

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    Heidelberg, 69120, Germany

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    Athens, 115 28, Greece

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    Athens, 11528, Greece

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    Heraklion, 71500, Greece

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    Bologna, 40139, Italy

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    Genova, 16132, Italy

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    Messina, 98125, Italy

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    Milan, 20133, Italy

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    Naples, 80131, Italy

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    Pavia, 27100, Italy

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    Roma, 00133, Italy

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    Roma, 00168, Italy

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    Lisbon, 1649 035, Portugal

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    Huelva, Andalusia, 21005, Spain

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    Palma de Mallorca, Balearic Islands, 07198, Spain

  • Study Center

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    Madrid, 28041, Spain

  • Study Centre

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    Sofia, 1431, Bulgaria

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    Égkomi, Nicosia, 2371, Cyprus

  • Study Centre

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    Nantes, 44093, France

  • Study Centre

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    Roma, Rome, 00189, Italy

  • Study Centre

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    Oviedo, Avenida de Roma, 33011, Spain

  • Study Centre

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    Villarreal, Barcelona, 08036, Spain

  • Study Centre

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    Barcelona, Catalonia, 08035, Spain

  • Study Centre

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    Madrid, Madrid, 28040, Spain

Conditions

Explore the condition pages connected to this study.