Gene therapy for rare blindness and deafness condition passes safety check
NCT ID NCT02065011
First seen Jan 21, 2026 · Last updated May 13, 2026 · Updated 20 times
Summary
This study looks at the long-term safety of a gene therapy called SAR421869 in 9 people with Usher syndrome type 1B, a rare genetic disorder that causes vision and hearing loss. Participants received the treatment in an earlier study and are now being followed to see if it remains safe and slows retinal degeneration. The goal is to understand if the therapy can help control the disease over time.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Investigational Site Number : 250001
Paris, 75012, France
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Oregon Health and Science University Site Number : 840001
Portland, Oregon, 97239-3098, United States
Conditions
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