Gene-Edited stem cells: a Long-Term watch for sickle cell patients

NCT ID NCT06155500

First seen Nov 01, 2025 · Last updated May 08, 2026 · Updated 29 times

Summary

This study follows 4 people with sickle cell disease who received a one-time treatment of gene-edited stem cells (OTQ923). The goal is to check for any delayed side effects and see how long the therapy's benefits last. Participants must have already completed at least one year of follow-up from the original treatment study.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Memorial Sloan Kettering Cancer Ctr

    New York, New York, 10065, United States

  • St Jude Childrens Research Hospital

    Memphis, Tennessee, 38105, United States

  • University of Chicago

    Chicago, Illinois, 60637, United States

Conditions

Explore the condition pages connected to this study.