Experimental epilepsy drug tested for long-term safety in children with rare sleep disorder

NCT ID NCT05301894

First seen Feb 23, 2026 · Last updated May 15, 2026 · Updated 12 times

Summary

This study looked at the long-term safety of an experimental drug called NBI-827104 in children with a rare form of epilepsy that causes continuous brain activity during sleep. The study enrolled 19 children and was terminated early. The main goal was to track serious side effects over time.

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Contacts and locations

Locations

  • Neurocrine Clinical Site

    Orange, California, 92868, United States

  • Neurocrine Clinical Site

    Aurora, Colorado, 80045, United States

  • Neurocrine Clinical Site

    Washington D.C., District of Columbia, 20010, United States

  • Neurocrine Clinical Site

    Miami, Florida, 33155, United States

  • Neurocrine Clinical Site

    Rochester, Minnesota, 55905, United States

  • Neurocrine Clinical Site

    Durham, North Carolina, 27705, United States

  • Neurocrine Clinical Site

    Cleveland, Ohio, 44195, United States

  • Neurocrine Clinical Site

    Dianalund, 4293, Denmark

  • Neurocrine Clinical Site

    Barcelona, 08950, Spain

  • Neurocrine Clinical Site

    Madrid, 28034, Spain

  • Neurocrine Clinical Site

    Zurich, 8032, Switzerland

  • Neurocrine Clinical Site

    London, WC1N 3JH, United Kingdom

Conditions

Explore the condition pages connected to this study.