Trikafta's long-term safety under the microscope for young CF patients

NCT ID NCT06460506

First seen Nov 01, 2025 · Last updated May 15, 2026 · Updated 24 times

Summary

This study looks at the long-term safety and effectiveness of the drug combination elexacaftor/tezacaftor/ivacaftor (known as Trikafta) in people with cystic fibrosis who are at least 12 months old. Participants must have completed a previous related study. The main goal is to track side effects and changes in sweat chloride levels, a key measure of CFTR function. This is an open-label study, meaning everyone knows they are receiving the active drug.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for CYSTIC FIBROSIS are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • Alder Hey Children's NHS Foundation Trust

    Liverpool, United Kingdom

  • British Columbia Children's Hospital

    Vancouver, Canada

  • Charité Universitätsmedizin BerlinX

    Berlin, Germany

  • Children and Young Adults Research Unit

    Cardiff, United Kingdom

  • Erasmus Medical Center

    Rotterdam, Netherlands

  • Great Ormond Street Hospital for Children

    London, United Kingdom

  • Inselspital - Universitaetsspital Bern

    Bern, Switzerland

  • Juliane Marie Center, Rigshospitalet

    Copenhagen, Denmark

  • Kinderklinik III, Abt. fur Pneumologie

    Essen, Germany

  • Kinderspital Zurich

    Zurich, Switzerland

  • Leeds General Infirmary

    Leeds, United Kingdom

  • Medizinische Hochschule Hannover

    Hanover, Germany

  • Queensland Children's Hospital

    South Brisbane, Australia

  • Royal Brompton Hospital

    London, United Kingdom

  • Southampton General Hospital

    Southampton, United Kingdom

  • The Hospital for Sick Children

    Toronto, Canada

  • The Kids Research Institute Australia

    Nedlands, Australia

  • The Royal Children's Hospital

    Parkville, Australia

Conditions

Explore the condition pages connected to this study.