Researchers track Long-Term safety of rare blood disorder treatment

NCT ID NCT07413679

Summary

This study is observing the long-term safety of adding a medication called danicopan to standard treatments for adults with paroxysmal nocturnal hemoglobinuria (PNH), a rare blood disease. It will follow about 50 patients already taking this combination therapy to monitor for serious side effects and infections. The goal is to better understand the safety profile of this treatment approach over time.

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Contacts and locations

Locations

  • Alexion Pharmaceuticals, Inc. (Sponsor)

    Boston, Massachusetts, 02210, United States

Conditions

Explore the condition pages connected to this study.