Researchers track Long-Term safety of rare blood disorder treatment

NCT ID NCT07413250

Summary

This study aims to understand the long-term safety of adding the drug danicopan to standard treatment for paroxysmal nocturnal hemoglobinuria (PNH), a rare blood disease. Researchers will analyze existing health data from about 50 adult patients already taking these medications. The goal is to monitor for side effects and complications over time to ensure the treatment remains safe for ongoing use.

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Contacts and locations

Locations

  • Clinical Research Site

    Boston, Massachusetts, 02210, United States

Conditions

Explore the condition pages connected to this study.