New study tracks Long-Term safety of danicopan combo for rare blood disorder

NCT ID NCT07413250

First seen Feb 24, 2026 · Last updated May 05, 2026 · Updated 9 times

Summary

This study looks at the long-term safety of adding danicopan to standard treatments (ravulizumab or eculizumab) for people with paroxysmal nocturnal hemoglobinuria (PNH), a rare blood disorder. Researchers will analyze data from 50 adults already enrolled in a PNH registry to track side effects, infections, and other health issues. The goal is to better understand the risks of this combination therapy over time.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Clinical Research Site

    Boston, Massachusetts, 02210, United States

Conditions

Explore the condition pages connected to this study.