New drug shows promise for children with dwarfism in Long-Term trial
NCT ID NCT02724228
First seen Mar 17, 2026 · Last updated May 21, 2026 · Updated 9 times
Summary
This study looks at the long-term safety and effectiveness of a daily injection called BMN 111 in 30 children with achondroplasia, the most common form of dwarfism. Participants had already received two years of treatment in an earlier study. Researchers are monitoring side effects and measuring growth over time to see if the drug helps improve height and body proportions.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Ann and Robert H. Lurie Childrens Hospital of Chicago
Chicago, Illinois, 60611, United States
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Baylor College of Medicine
Houston, Texas, 77030, United States
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Children's Hospital & Research Center Oakland
Oakland, California, 94609, United States
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Guys & St. Thomas NHS Foundation Trust Evelina Hospital
London, SE1 9RT, United Kingdom
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Harbor - UCLA Medical Center
Torrance, California, 90509, United States
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Institut Necker
Paris, 75015, France
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Johns Hopkins McKusick - Institute of Genetic Medicine
Baltimore, Maryland, 21287, United States
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Murdoch Children's Research Institute
Parkville, Victoria, 3052, Australia
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Vanderbilt University
Nashville, Tennessee, 37232-2578, United States
Conditions
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