Gene therapy for cystic fibrosis: 15-Year safety watch begins

NCT ID NCT06962852

First seen Nov 01, 2025 · Last updated May 11, 2026 · Updated 21 times

Summary

This study follows 5 people with cystic fibrosis who received a single dose of BI 3720931 gene therapy in an earlier trial. Participants do not receive any new treatment. Doctors will check their health and lung function for up to 15 years to see if the therapy remains safe and effective over time.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for CYSTIC FIBROSIS are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • Hospital Universitari Vall d'Hebron

    Barcelona, 08035, Spain

  • Hôpital Gui de Chauliac

    Montpellier, 34295, France

  • Osp. Pediatrico Bambin Gesù

    Roma, 00165, Italy

  • Royal Brompton Hospital

    London, SW3 6JY, United Kingdom

  • Universitair Medisch Centrum Utrecht

    Utrecht, 3584 CX, Netherlands

Conditions

Explore the condition pages connected to this study.