Terminated trial offered continued access to rare blood disorder drug

NCT ID NCT05741346

Summary

This study provided continued access to the experimental drug BCX9930 for 28 people with paroxysmal nocturnal hemoglobinuria (PNH), a rare and serious blood disorder. Participants had previously benefited from BCX9930 in earlier studies and didn't have other treatment options. The main goal was to monitor the long-term safety of continued BCX9930 treatment for up to 96 weeks, though the study was ultimately terminated.

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Contacts and locations

Locations

  • Investigative Site

    Paris, France

  • Investigative Site

    Budapest, Hungary

  • Investigative Site

    Ampang, Malaysia

  • Investigative Site

    Bloemfontein, South Africa

  • Investigative Site

    Cape Town, South Africa

  • Investigative Site

    Pretoria, South Africa

  • Investigative Site

    Daejeon, South Korea

  • Investigative Site

    Barcelona, Spain

  • Investigative Site

    Valencia, Spain

  • Investigative Site

    Leeds, United Kingdom

  • Investigative Site

    London, United Kingdom

Conditions

Explore the condition pages connected to this study.