Five-Year hunt for hunter syndrome treatment safety
NCT ID NCT06075537
Summary
This study continues testing an experimental enzyme replacement therapy called DNL310 in people with Hunter syndrome (MPS II) who completed previous trials. It aims to understand the long-term safety and effectiveness of this treatment when given for up to five years. The therapy is designed to reach both the body and brain to address symptoms of this rare genetic disorder.
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Contacts and locations
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Locations
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ASST di Cremona
Cremona, Italy
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Azienda Sanitaria Universitaria Friuli Centrale - PO Universitario Santa Maria della Misericordia
Udine, Italy
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Birmingham Women's and Children's NHS Foundation Trust
Birmingham, United Kingdom
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Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
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Cincinnati Children's Hospital Medical Center
Cincinnati, Ohio, 45229, United States
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Drottning Silvias Barn Och Ungdomssjukhus
Gothenburg, Sweden
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Erasmus Medical Center - Sophia Children's Hospital
Rotterdam, 3015 GD, Netherlands
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Gazi Universitesi Tip Fakultes
Ankara, Turkey (Türkiye)
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Great Ormond Street Hospital
London, WC1N 3JH, United Kingdom
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Hopital Jeanne De Flandre - Metabolic Diseases Unit
Lille, France
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Hospit U. Vall d'Hebron - PPDS
Barcelona, Spain
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Hospital for Sick Children
Toronto, Ontario, M5G 1X8, Canada
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Huntsman Cancer Hospital
Salt Lake City, Utah, 84112, United States
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McGill University Health Center
Montreal, Quebec, H4A3J1, Canada
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Sanatorio Mater Dei
Buenos Aires, Argentina
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SpinCS GmbH
Höchheim, Germany
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The University of Texas Medical School at Houston
Houston, Texas, 77030, United States
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UCSF Benioff Children's Hospital Oakland
Oakland, California, 94609, United States
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UNC Children's Research Institute
Chapel Hill, North Carolina, 27599, United States
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UZ Brussel
Jette, Belgium
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Universitair Ziekenhuis Antwerpen
Edegem, Antwerpen, 2650, Belgium
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University Medical Faculty Balcali Hospital
Adana, Turkey (Türkiye)
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University of Alberta - Faculty of Medicine & Dentistry
Edmonton, Alberta, Canada
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Universitätsklinikum Hamburg-Eppendorf
Hamburg, Germany
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Vseobecna Fakultni Nemocnice V Praze
Prague, 120 00, Czechia
Conditions
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