Gene therapy for hemophilia b: tracking Long-Term results in 500 patients

NCT ID NCT06008938

Summary

This study follows 500 people with hemophilia B who have received HEMGENIX gene therapy to understand its long-term effectiveness and safety. Researchers will track how many bleeding episodes patients experience and compare results to those receiving standard preventive treatments. The goal is to gather real-world evidence about how well this one-time gene therapy controls bleeding over many years.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Aarhus Universitetshospital

    RECRUITING

    Århus N, Denmark

  • American Thrombosis and Hemostasis Network

    RECRUITING

    Rochester, New York, 14604, United States

  • CHU Nancy - Hôpital Brabois

    RECRUITING

    Vandœuvre-lès-Nancy, France

  • Centre Hospitalier Universitaire de Brest / CHU Morvan

    RECRUITING

    Brest, France

  • Centre Régional de Traitement de l'Hémophilie

    RECRUITING

    Nantes, France

  • Hannover Medical School

    RECRUITING

    Hanover, Germany

  • Hospital Alvaro Cunqueiro Dr. Manuel Rodriquez-Lopez

    RECRUITING

    Vigo, Spain

  • Klinik für Angiologie/ Hämostaseologie

    RECRUITING

    Berlin, Germany

  • Klinikum der Johann-Wolfgang Goethe Universitaet

    RECRUITING

    Frankfurt, Germany

  • Medical University Vienna

    RECRUITING

    Vienna, Austria

  • University Hospital Bern Inselspital

    RECRUITING

    Bern, Switzerland

  • University of Clinic Bonn

    RECRUITING

    Bonn, Germany

Conditions

Explore the condition pages connected to this study.