Heart Drug's Long-Term safety under the microscope in major study
NCT ID NCT04848506
Summary
This study aims to gather long-term safety information on the experimental drug aficamten for people with symptomatic hypertrophic cardiomyopathy (HCM), a condition where the heart muscle thickens. It will follow 900 participants who have already taken aficamten in a previous trial to monitor for any side effects over an extended period. The main goal is to see how safe and well-tolerated the drug is with continued use.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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"Hippokration" General Hospital of Athens
Athens, 11527, Greece
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ASST Grande Ospedale Metropolitano Niguarda
Milan, 20162, Italy
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Alaska Heart and Vascular Institute
Anchorage, Alaska, 99508, United States
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Amsterdam UMC
Amsterdam, 1105, Netherlands
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Ascension Saint Thomas Heart West
Nashville, Tennessee, 37205, United States
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Ascension St. John Clinical Research Institute
Tulsa, Oklahoma, 76104, United States
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Aurora St. Luke's Medical Center
Milwaukee, Wisconsin, 53215, United States
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Azienda Ospedaliera Universitaria Federico II di Napoli
Naples, 80131, Italy
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Azienda Sanitaria Universitaria Giuliano Isontina
Trieste, 34149, Italy
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Brigham and Women's Hospital
Boston, Massachusetts, 02115, United States
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CHI St. Luke's Health Baylor College of Medicine Medical Center
Houston, Texas, 77030, United States
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CHU Montpellier - Hopital Arnaud de Villeneuve
Montpellier, 34295, France
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CHU de Nantes Institut Du Thorax et du systeme nerveux Clinique Cardiologique et des Maladies Vasculaires
Nantes, 44093, France
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Cedar-Sinai Medical Center
Los Angeles, California, 90048, United States
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Cedars-Sinai Medical Center (Smidt Heart Institute)
Los Angeles, California, 90048, United States
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Centre Hospitalier universitaire de Toulouse - Rangueil Hospital
Toulouse, 31059, France
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Centre hospitalier universitaire (CHU) de Rennes-Hopital Pontchaillou
Rennes, 35033, France
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Centro Hospitalar Do Baixo Vouga, EPE Cardiology Department
Aveiro, 3814-501, Portugal
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Charite-Universitaetsmedizin Berlin
Berlin, 13353, Germany
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Cleveland Clinic
Cleveland, Ohio, 44195, United States
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Clinique Du Millenaire
Montpellier, 340000, France
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Columbia University Medical Center/New York Presbyterian Hospital
New York, New York, 10032, United States
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Complejo Hospitalario Universitario A Coruna
A Coruña, 15006, Spain
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Complexo Hospitalario Universitario De Vigo
Pontevedra, 36312, Spain
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Copenhagen University Hospital
Copenhagen, 2400, Denmark
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Department of Cardiology Aalborg University Hospital
Aalborg, 9000, Denmark
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Department of Cardiology Aarhus University Hospital
Aarhus, 8200, Denmark
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Dipartimento di Medicina Clinica e Molecolare Universita Sapienza di Roma Unita di Terapia Intensiva Cardiologica Azienda Ospedaliero Universitaria Sant'Andrea
Roma, 00189, Italy
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Duke Cardiology at Southpoint
Durham, North Carolina, 27710, United States
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Emory Clinic
Atlanta, Georgia, 30322, United States
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Erasmus Medical Center Department of Cardiology
Rotterdam, 3015, Netherlands
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Evangelismos General Hospital of Athens
Athens, 10676, Greece
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Fiona Stanley Hospital, AHF Unit
Murdoch, 6150, Australia
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Flinders Medical Centre, Cardiology Research
Bedford Park, 5042, Australia
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Fondazione toscana Gabriele Monesterio per la ricarca medica Dipartimento Cardiotoracico UOC Cardiologia e Medicina Cardiovasculare Ospedale San Cataldo
Pisa, 56124, Italy
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Glasgow Clinical Research Facility Neuroscience Institute
Glasgow, G51 4TF, United Kingdom
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Greenville Memorial Hospital
Greenville, South Carolina, 29605, United States
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Hadassah Medical Center- Ein Kerem
Jerusalem, 9112001, Israel
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Henry Ford Hospital
Detroit, Michigan, 48202, United States
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Holy Cross Hospital / Cardiology Associates
Fort Lauderdale, Florida, 33308, United States
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Hopital Europeen Georges Pompidou
Paris, 75015, France
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Hopital Lariboisiere
Paris, 75010, France
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Hopital cardiologique de Haut-Leveque
Pessac, 33604, France
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Hopital de la Timone Service de cardiologie
Marseille, 130005, France
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Hospital Clinic Barcelona
Barcelona, 08036, Spain
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Hospital Clinico Universitario San Carlos
Madrid, 28040, Spain
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Hospital Clinico Universitario Virgen de la Arrixaca
Madrid, 30120, Spain
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Hospital Cuf Descobertas S.A.
Lisbon, 1998-018, Portugal
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Hospital General Universitario Gregorio Marañón (HGUGM)
Madrid, 28007, Spain
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Hospital Universitario Puerta de Hierro Majadahonda
Madrid, 28220, Spain
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Hospital Universitario Son Llatzer
Palma, 07198, Spain
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Hospital Universitario Virgen Macarena-merge
Seville, 41009, Spain
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Hospital Universitario Virgen de la Victoria
Málaga, 29010, Spain
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Hospital Universitario Virgen del Rocío
Seville, 41013, Spain
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Hospital Universitario de Salamanca
Salamanca, 37007, Spain
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Hospital da Luz
Lisbon, Portugal
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Hospital of the University of Pennsylvania (University of Pennsylvania School of Medicine)
Philadelphia, Pennsylvania, 19104, United States
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Houston Methodist Hospital
Houston, Texas, 77030, United States
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IRCCS Policlinico San Donato
Milan, 20097, Italy
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Il. Interni klinika kardiologie a angiologie
Prague, 128 08, Czechia
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Inova Health Care Services
Falls Church, Virginia, 22042, United States
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Institut universitaire de cardiologie et de pneumologie de Quebec-Universite Laval
Québec, Quebec, G1V 4G5, Canada
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Instituto Cardiovascular de Buenos Aires(ICBA)
Buenos Aires, C1428, Argentina
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Instituto Dante Pazzanese de Cardiologia
São Paulo, 04012-909, Brazil
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Intermountain Medical Center
Murray, Utah, 84107, United States
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Kardio Brynow S.C.
Katowice, 40-555, Poland
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Lahey Hospital & Medical Center
Burlington, Massachusetts, 01805, United States
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Landspitali University Hospital
Reykjavik, 101, Iceland
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Liverpool Heart and Chest Hospital
Liverpool, L14 3PE, United Kingdom
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Maastricht University Medical Center (MUMC)
Maastricht, 6229 HX, Netherlands
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Massachusetts General Hospital
Boston, Massachusetts, 02114, United States
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Mayo Clinic Building - Phoenix
Phoenix, Arizona, 85054, United States
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MedStar Washington Hospital Center
Washington D.C., District of Columbia, 20010, United States
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Medical University of South Carolina
Charleston, South Carolina, 29425, United States
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Meir Medical Center
Kfar Saba, 4428164, Israel
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Michigan Medicine - University of Michigan
Ann Arbor, Michigan, 48109, United States
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Morristown Medical Center
Morristown, New Jersey, 07960, United States
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Mount Sinai Hospital
New York, New York, 10029, United States
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NYU Langone Health
New York, New York, 10016, United States
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Narodowy Instytut Kardiologii Stefana Kardynala Wyszynskiego - Panstwowy Instytut Badawczy Centrum Zaburzen Rytmu Serca
Warsaw, 04-628, Poland
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Ninewells Hospital and Medical School
Dundee, DD2 1SG, United Kingdom
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Northwell Health North Shore University Hospital
Manhasset, New York, 11030, United States
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Northwestern University
Evanston, Illinois, 60208, United States
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Odense University Hospital
Odense, 5000, Denmark
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Onassis Hospital
Athens, 17674, Greece
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Oregon Health & Science University
Portland, Oregon, 97239, United States
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Oxford Centre for Clinical Magnetic Resonance Research (OCMR) Division of Cardiovascular Medicine Radcliffe Department of Medicine University of Oxford
Oxford, OX3 9DU, United Kingdom
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Piedmont Fayette Hospital
Fayetteville, Georgia, 30214, United States
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Providence St. Vincent Medical Center
Portland, Oregon, 97225, United States
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QEII Health Science Centre (Halifax Infirmary site)
Halifax, B3H 3A7, Canada
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Queen Elizabeth Hospital Birmingham University Hospitals Birmingham NHS Foundation Trust
Birmingham, B15 2GW, United Kingdom
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Royal Alexandra Hospital
Edmonton, T5H 3V9, Canada
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Royal Brompton Hospital
London, SW3 6NP, United Kingdom
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Saint Luke's Hospital of Kansas City
Kansas City, Missouri, 64111, United States
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Sanger Heart & Vascular Institute - HCM Clinic
Charlotte, North Carolina, 28204, United States
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Semmelweis Egyetem Varosmajori Sziv es Ergyogyaszati Klinika
Budapest, 1122, Hungary
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St Bartholomew's Hospital
London, EC1A 7BE, United Kingdom
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St George's University Hospitals NHS Foundation Trust
London, SW17 0QT, United Kingdom
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Szegedi Tudományegyetem, Belgyógyászati Klinika, Kardiológiai Központ
Szeged, 6725, Hungary
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The Barzilai University Medical Center
Ashkelon, 7830604, Israel
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The Chaim Sheba Medical Center
Ramat Gan, 5265601, Israel
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The Heart Center, Department of Cardiology
Copenhagen, 2100, Denmark
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The Linder Research Center at The Christ Hospital
Cincinnati, Ohio, 45219, United States
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The Prince Charles Hospital
Chermside, 4032, Australia
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The University of Kansas Medical Center
Kansas City, Kansas, 66160, United States
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The University of Texas Southwestern Medical Center at Dallas
Dallas, Texas, 75390, United States
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UC San Diego Health - Sulpizio Cardiovascular Center
La Jolla, California, 92037, United States
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UCSF Medical Center
San Francisco, California, 94143, United States
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UPMC Presbyterian
Pittsburgh, Pennsylvania, 15213, United States
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Unidade Local De Saude De Sao Jose E.P.E
Lisbon, 1150-199, Portugal
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Unit Cardiomiopatie, Dipartimento Cardio ToracoVascolare
Florence, 50134, Italy
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Universitaesklinkum Heidelberg
Heidelberg, 69120, Germany
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Universitaetskinikum Wuerzburg Deutsches Zentrum fur Herzinsuffzienz Wurzburg (DZHI) Comprehensive Heart Failure Center (CHFC)
Würzburg, 97078, Germany
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Universitaetsklinikum Essen
Essen, 45147, Germany
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Universitaetsklinikum Jena
Jena, 07747, Germany
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Universitaetsmedizin Goettingen Klinik fur Kardiologie und Pneumologie
Goettigen, 37075, Germany
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University General Hospital "ATTIKON"
Attiki, 12462, Greece
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University Hospitals Cleveland Medical Center
Cleveland, Ohio, 44106, United States
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University of Alabama at Birmingham
Birmingham, Alabama, 35233, United States
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University of Michigan Health System (UMHS) - University Hospital (University of Michigan Medical Center)
Ann Arbor, Michigan, 48109, United States
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University of Utah Health
Salt Lake City, Utah, 84132, United States
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University of Virginia Health System University Hospital
Charlottesville, Virginia, 22908, United States
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Vanderbilt University Medical Center
Nashville, Tennessee, 37232, United States
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Virginia Mason Medical Center
Seattle, Washington, 98101, United States
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WVUMedicine
Morgantown, West Virginia, 26506, United States
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Weill Cornell Medicine
New York, New York, 10021, United States
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Westchester Medical Center
Valhalla, New York, 10595, United States
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Yale New Haven Hospital
New Haven, Connecticut, 06519, United States
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Ziv Medical Center
Safed, 1311001, Israel
Conditions
Explore the condition pages connected to this study.