Extended trial tests daily shots to boost growth in kids with dwarfism
NCT ID NCT02724228
Summary
This study follows children with achondroplasia, a genetic condition that causes short stature, to see how safe and effective a daily injection called BMN 111 is over a longer period. It includes about 30 children who have already been taking the drug for two years in a previous study. The main goal is to check for any long-term side effects while also measuring if the treatment continues to help children grow taller and improve their body proportions.
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Contacts and locations
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Locations
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Ann and Robert H. Lurie Childrens Hospital of Chicago
Chicago, Illinois, 60611, United States
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Baylor College of Medicine
Houston, Texas, 77030, United States
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Children's Hospital & Research Center Oakland
Oakland, California, 94609, United States
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Guys & St. Thomas NHS Foundation Trust Evelina Hospital
London, SE1 9RT, United Kingdom
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Harbor - UCLA Medical Center
Torrance, California, 90509, United States
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Institut Necker
Paris, 75015, France
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Johns Hopkins McKusick - Institute of Genetic Medicine
Baltimore, Maryland, 21287, United States
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Murdoch Children's Research Institute
Parkville, Victoria, 3052, Australia
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Vanderbilt University
Nashville, Tennessee, 37232-2578, United States
Conditions
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