Extended hope: DMD drug GIVINOSTAT gets Long-Term safety check

NCT ID NCT03373968

Recruiting now Disease control Sponsor: Italfarmaco Source: ClinicalTrials.gov ↗

Summary

This study aims to understand the long-term safety and effectiveness of the drug GIVINOSTAT in boys with Duchenne muscular dystrophy (DMD). It is open to about 206 participants, aged 6 and older, who have already taken GIVINOSTAT in a previous related study. The main goal is to monitor for side effects and see how well the drug continues to work over a longer period.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

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Study contacts

Contact

Phone: •••-•••-•••• Email: •••••@•••••

Locations

A.O.U. Policlinico G. Martino, U.O.C. Neurologia e Malattie Neuromuscolari
ENROLLING_BY_INVITATION

Messina, 98125, Italy
Alder Hey Children's Hospital NHS Trust
ENROLLING_BY_INVITATION

Liverpool, UK, L12 2AP, United Kingdom
CHU de Nantes - Hotel-Dieu - Hopital Nord Laennec, rez-de-chausse haut ail Ouest
ENROLLING_BY_INVITATION

Nantes, 44093, France
Centro Clinico NeMO Fondazione Serena ONLUS Area SUD
ENROLLING_BY_INVITATION

Milan, 20162, Italy
Child Health Research Institute
COMPLETED

Gainesville, Florida, 32610, United States
Clinic of Neurology and Psychiatry for Children and Youth - Neurology Department Dr. Subotic 6a,
ENROLLING_BY_INVITATION

Belgrade, 11000, Serbia
Connecticut Children's Medical Center, Neurology Division
COMPLETED

Hartford, Connecticut, 06106, United States
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano, UOS di Neurologia Pediatrica
ACTIVE_NOT_RECRUITING

Milan, 20122, Italy
Fondazione Policlinico Universitario "A.Gemelli", UOC Neuropsichiatria Infantile
ENROLLING_BY_INVITATION

Roma, 00168, Italy
Holland Bloorview Kids Rehabilitation Hospital
ENROLLING_BY_INVITATION

Toronto, Ontario, M4G1R8, Canada
Hospital Materno-Infantil
RECRUITING

Barcelona, 08035, Spain

Contact Email: •••••@•••••

Contact
Hospital Universitari i Politècnic La Fe - Servicio Neurologia
ENROLLING_BY_INVITATION

Valencia, Spain
Hospital Universitario Virgen del Rocio
ENROLLING_BY_INVITATION

Seville, 41013, Spain
Hospital de La Citadelle, Centre de Référence des Maladies Neuromuscolaires (CRMN)
ENROLLING_BY_INVITATION

Liège, 04000, Belgium
Hôpital Armand Trousseau I-Motion - Plateforme d'essais cliniques pédiatriques Bâtiment Lemariey - Porte 20 * 2ème étage 26 Avenue du Dr Arnold Nette
ENROLLING_BY_INVITATION

Paris, 760, France
IRCCS Istituto Neurologico Carlo Besta
ENROLLING_BY_INVITATION

Milan, 20133, Italy
Institute of Neurology - Schneider Children's Medical Center of Israel Kaplan, 14
ENROLLING_BY_INVITATION

Petah Tikva, 4920235, Israel
Kinsmen Research Centre - Alberta Children's Hospital
ENROLLING_BY_INVITATION

Calgary, Alberta, T3B 6A8, Canada
Klinik- und Poliklinik fur Kinder- und Jugendmedizin, Universitatsklinikum HamburgEppendorf, Martinistr. 52
ENROLLING_BY_INVITATION

Hamburg, 20246, Germany
Klinikum der Universitat Munchen, Campus Innenstadt, Lindwurmstr. 4
ACTIVE_NOT_RECRUITING

München, 80337, Germany
Leiden University Medical Center LUMC, Albinusdreef 2
ENROLLING_BY_INVITATION

Leiden, 2300, Netherlands
MD Rare Disease Research, LLC
ENROLLING_BY_INVITATION

Atlanta, Georgia, 30318, United States
Neuromuscular Pathology Unit - Hospital Sant Joan de Déu
ENROLLING_BY_INVITATION

Esplugues de Llobregat, Barcellona, 08950, Spain
Ospedale Pediatrico Bambino Gesù, Malattie Neuromuscolari e Neurodegenerative
RECRUITING

Roma, 00146, Italy

Contact Email: •••••@•••••

Contact
Radboud University Medical Centre
ENROLLING_BY_INVITATION

Nijmegen, 6500, Netherlands
Rady Children's Hospital center - UCSD Department of Neuroscience
COMPLETED

San Diego, California, 92123, United States
Shriners Hospitals for Children
COMPLETED

Portland, Oregon, 97239, United States
The Children's Hospital of Philadelphia Colket Translational Research Building
COMPLETED

Philadelphia, Pennsylvania, 19104, United States
The John Walton Muscular Dystrophy Research Centre
ENROLLING_BY_INVITATION

Newcastle upon Tyne, NE1 3BZ, United Kingdom
The Robert Jones and Agnes Hunt Orthopaedic Hospital NHS Foundation Trust
ENROLLING_BY_INVITATION

Gobowen, SY10 7AG, United Kingdom
The University of British Columbia, Children's and Womens Health Centre of BC Branch
ENROLLING_BY_INVITATION

Vancouver, British Columbia, V6H 3V4, Canada
U.O.S.D. Centro Traslazionale di Miologia e Patologie Neurodegenerative, Building 16 - ground floor IRCCS Istituto Giannina Gaslini,
RECRUITING

Genova, 16147, Italy

Contact Phone: •••-•••-•••• Email: •••••@•••••

Contact
UCL Great Ormond Street Institute of Child Health, Dubowitz Neuromuscular Centre and MRC Centre for NMD
ENROLLING_BY_INVITATION

London, , WC1N 1EH, United Kingdom
University Hospitals Leuven, Neuromuscular Reference Centre, Child Neurology
ENROLLING_BY_INVITATION

Leuven, 03000, Belgium
University of California - Davis Medical Center - Devis Physical Medicine & Rehabilitation
COMPLETED

Sacramento, California, 95817, United States
University of Iowa Children's Hospital
ENROLLING_BY_INVITATION

Iowa City, Iowa, 52242, United States
Universitätsklinikum Essen - Kinder-und Jugendmedizin Neuropadiatrie
ENROLLING_BY_INVITATION

Essen, D-45147, Germany
Virginia Commonwealth University Childrens Hospital of Richmond at
COMPLETED

Richmond, Virginia, 23298, United States
Washington University School of Medicine in St Louis Department of Neurology 660 S.Euclid Avenue, Campus Box 8111
COMPLETED

St Louis, Missouri, 63110, United States

Conditions

Explore the condition pages connected to this study.

DUCHENNE MUSCULAR DYSTROPHY