Extended hope for rare neurological disease
NCT ID NCT05515536
Summary
This study aims to see if the drug vatiquinone is safe and effective for people with Friedreich ataxia when taken for up to three years. It is for 130 participants who have already been taking vatiquinone in a previous trial. The main goal is to monitor for side effects while also checking if the drug helps slow the progression of the disease.
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Contacts and locations
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Locations
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CBR Neurogenetic Research Clinic, University of Auckland
Auckland, 1023, New Zealand
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CHU Sainte-Justine
Montreal, Quebec, H3T1C5, Canada
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Centre de Recherche du Centre Hospitalier de l'Université de Montreal (CRCHUM)
Montreal, Quebec, H2X 0A9, Canada
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Department of Neurology and Hertie-Institute for Clinical Brain Research German Center of Neurodegenerative Diseases (DZNE)
Tübingen, 72076, Germany
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Hospital Sant Joan de Déu Barcelona Unidad de Enfermedades Neuromusculares
Barcelona, 08950, Spain
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Hôpital Pitié-Salpêtrière, Institut du Cerveau (Paris Brain Institute)
Paris, 75646, France
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Murdoch Children's Research Institute
Parkville, Victoria, 3052, Australia
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Ospedale Pediatrico Bambino Gesu' IRCCS
Roma, 00165, Italy
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The Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
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UCLA
Los Angeles, California, 90095, United States
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University of Campinas (UNICAMP) - School of Medical Sciences, Dept of Neurology
São Paulo, 13083-887, Brazil
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University of Florida
Gainesville, Florida, 32608, United States
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University of Iowa
Iowa City, Iowa, 52242, United States
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University of South Florida
Tampa, Florida, 33612, United States
Conditions
Explore the condition pages connected to this study.