Gene therapy for rare blindness passes 5-Year safety check
NCT ID NCT04312672
First seen Nov 01, 2025 · Last updated May 23, 2026 · Updated 20 times
Summary
This study followed 42 people with X-linked retinitis pigmentosa, an inherited eye disease that causes vision loss, for up to 5 years after they received a gene therapy. The goal was to check the long-term safety of the treatment and see if it helped with functional vision, like walking in low light. Participants had already received the gene therapy in an earlier trial.
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the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Leeds Teaching Hospitals NHS Trust
Leeds, LS9 7TF, United Kingdom
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Massachusetts Eye and Ear Infirmary
Boston, Massachusetts, 02114, United States
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Moorfields Eye Hospital
London, EC1V 9EL, United Kingdom
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Univ of Michigan Medical Center
Ann Arbor, Michigan, 48105, United States
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University of Pittsburgh Medical Center
Pittsburgh, Pennsylvania, 15213, United States
Conditions
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