Gene therapy for HAE: Long-Term Follow-Up begins
NCT ID NCT06262399
First seen Jan 06, 2026 · Last updated May 24, 2026 · Updated 15 times
Summary
This study follows 100 people with hereditary angioedema (HAE) who previously received the experimental gene therapy NTLA-2002. Researchers will track side effects and how well the treatment controls swelling attacks over time. The goal is to understand the long-term safety and lasting benefits of this one-time therapy.
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This is a summary of
the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Cambridge University Hospitals NHS Foundation Trust, Addenbrooke's Hospital
Cambridge, United Kingdom
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Campbelltown Hospital
Campbelltown, New South Wales, 2560, Australia
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Centre National de Reference - Grenoble
Grenoble, France
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Charite-Universitätsmedizin Berlin
Berlin, 12203, Germany
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Hôpital Claude Huriez
Lille, 59037, France
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New Zealand Clinical Research
Auckland, New Zealand
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University of Amsterdam Academic Medical Center
Amsterdam, Netherlands
Conditions
Explore the condition pages connected to this study.