Fabry disease treatment faces Long-Term safety check

NCT ID NCT03737214

Summary

This study follows adults with Fabry disease who previously took lucerastat in an earlier trial. Researchers want to understand the long-term safety and side effects of continuing this oral medication. The study will monitor participants for up to 8 years or until the drug becomes commercially available.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for FABRY DISEASE are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • Baylore University Medical Center

    Dallas, Texas, 75246, United States

  • Children's Hospital Research Institute of Manitoba

    Winnipeg, R3E 3P4, Canada

  • Clinic of Immunological Diseases and Blood Coagulability Cracow University Hospital

    Krakow, 31-066, Poland

  • Greenwood Genetics Center

    Greenville, South Carolina, 29605, United States

  • Haukeland University Hospital

    Bergen, 5021, Norway

  • Hospital Academisch Medisch Centrum - Department of Internal Medicine, Div. Endrocrinology and Metabolism

    Amsterdam, 1105 AZ, Netherlands

  • Hospital Quironsalud Zaragoza

    Zaragoza, 50012, Spain

  • Hospital Universitari de Bellvitge / Nephrology Dpt

    Barcelona, 08907, Spain

  • Hospital Universitario Ramon y Cajal. Servicio de Medicina Interna

    Madrid, 28034, Spain

  • Infusion Associates

    Grand Rapids, Michigan, 49525, United States

  • London Health Sciences CTR, Victoria Hospital

    London, N6A 5W9, Canada

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc.

    Fairfax, Virginia, 22030, United States

  • Massachusetts General Hospital

    Boston, Massachusetts, 02114, United States

  • Medizinische Universität Wien, Universitätsklinik für Innere Medizin III, Klinische Abteilung für Nephrologie und Dialyse

    Vienna, 1090, Austria

  • Narodowy Instytut Kardiologii Stefana kardynała Wyszyńskiego - Państwowy Instytut Badawczy

    Warsaw, 04-628, Poland

  • National Hospital for Neurology and Neurosurgery

    London, WC1N 3BG, United Kingdom

  • Nephrologicum Markgräflerland MVZ GmbH

    Müllheim, 79379, Germany

  • Psychiatrische Universitätsklinik Zürich

    Zurich, 8032, Switzerland

  • Raymond Poincaré Hosp - Med Genetics Dept

    Garches, 92380, France

  • Renal Disease Research Institute LLC

    Dallas, Texas, 75204, United States

  • Research Center, Hôpital du Sacré-Coeur de Montréal

    Montreal, H4J 1C5, Canada

  • Royal Free London NHS Foundation Trust Lysosomal Storage Disorder Unit; Department of Hematology

    London, NW3 2QG, United Kingdom

  • Royal Melbourne Hospital - Department of Nephrology

    Parkville, 3050, Australia

  • Royal Perth Hospital, Department of Nephrology

    Perth, Perth, 6000, Australia

  • Rush University Medical Center - Dept of Pediatrics

    Chicago, Illinois, 60612, United States

  • Salford Hospital

    Manchester, M6 8HD, United Kingdom

  • SphinCS GmbH

    Höchheim, 65239, Germany

  • The Children's Memorial Health Institute, Department of Pediatric, Nutrition and Metabolic Diseases

    Warsaw, 04-730, Poland

  • UCSF Benioff Children's Hospital Oakland

    Oakland, California, 94609, United States

  • University Hospital Gasthuisberg, Leuven (UZ Leuven)

    Leuven, 3000, Belgium

  • University Hospital Ghent (UZ Ghent)

    Ghent, 9000, Belgium

  • University of Alabama at Birmingham - Nephrology Research Clinic

    Birmingham, Alabama, 35294, United States

  • University of Calgary - Heritage Medical Research Clinic

    Calgary, T2N 4Z6, Canada

  • University of California Irvine

    Irvine, California, 92697, United States

  • University of Florida Clinical and Translational Science Institute, UF Clinical Research Center

    Gainesville, Florida, 32610, United States

  • University of Iowa Stead Family Children's Hospital - Division of Medical Genetics

    Iowa City, Iowa, 52242, United States

  • University of Pennsylvania - Dept of Medicine

    Philadelphia, Pennsylvania, 19104, United States

  • University of Utah - Division of Medical Genetics, Clinical Genetics Research

    Salt Lake City, Utah, 84108, United States

  • Universitätsklinikum Würzburg

    Würzburg, 97080, Germany

  • Universitätsmedizin Berlin - Charité Campus Mitte

    Berlin, 10117, Germany

  • Vall d'Hebron University Hospital - Unit of Inherited Metabolic Disorders and Rare Diseases

    Barcelona, 08035, Spain

  • Vancouver General Hospital - Adult Metabolic Diseases Clinic

    Vancouver, V5Z 1M9, Canada

Conditions

Explore the condition pages connected to this study.