New study tracks growth in kids with rare disease on enzyme therapy
NCT ID NCT02455622
First seen Apr 05, 2026 · Last updated May 16, 2026 · Updated 8 times
Summary
This study followed 21 children with Hunter Syndrome who started treatment with Elaprase before age 6. Researchers measured changes in height and weight over time to see how the drug affected growth. The study also monitored safety and compared results to untreated patients from a registry.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Ann & Robert H. Lurie Children's Hospital of Chicago
Chicago, Illinois, 60611, United States
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Chulalongkorn University
Bangkok, 10330, Thailand
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Hospital Infantil Dr Robert Reid Cabral
Santo Domingo, 10101, Dominican Republic
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Hospital Kuala Lumpur
Kuala Lumpur, 50586, Malaysia
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Mother and Child Health Care Institute of Serbia Dr Vukan Cupic
Belgrade, 11000, Serbia
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National Pediatrics Hospital
Hanoi, Vietnam
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Philippine General Hospital
Manila, 1000, Philippines
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Universitätsmedizin der Johannes Gutenberg-Universität Mainz
Mainz, 55131, Germany
Conditions
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