Tracking the future: Long-Term study for duchenne gene therapy patients
NCT ID NCT05967351
Summary
This study is tracking the long-term safety and effectiveness of a gene therapy called delandistrogene moxeparvovec (SRP-9001) in people with Duchenne muscular dystrophy. It will follow 400 participants who have already received the therapy in a previous clinical trial. The goal is to see how well the treatment continues to work and monitor for any long-term side effects over time.
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Contacts and locations
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Locations
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Ann & Robert H. Lurie Children's Hospital of Chicago
Chicago, Illinois, 60611, United States
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Arkansas Children's Hospital
Little Rock, Arkansas, 72202, United States
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Boston Children's Hospital
Boston, Massachusetts, 02115, United States
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Chiildren's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
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Children's Health Specialty Center
Dallas, Texas, 75207, United States
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Children's Hospital Wisconsin
Milwaukee, Wisconsin, 53226, United States
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Children's Hospital of Colorado
Aurora, Colorado, 80045-7106, United States
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Children's Hospital of The King's Daughters
Norfolk, Virginia, 23510, United States
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Columbia University Pediatric Neuromuscular Center
New York, New York, 10032, United States
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Great Ormond Street Hospital For Children NHS Foundation Trust
London, Greater London, WC1N 1EJ, United Kingdom
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Hong Kong Children's Hospital
Hong Kong, Hong Kong
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Hospital Sant Joan de Deu
Esplugues de Llobregat, Barcelona, 08950, Spain
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Hospital Universitario y Politecnico La fe. Neurology Department
Valencia, 46026, Spain
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Institute of Translational and Clinical Research
Newcastle upon Tyne, NE1 3BZ, United Kingdom
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Kaohsiung Medical University Chung-Ho Memorial Hospital
Kaohsiung City, 807, Taiwan
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Kobe University Hospital
Kobe, Hyōgo, 650-0017, Japan
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Lenox Baker Children's Hospital (Duke University)
Durham, North Carolina, 27705, United States
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Lucile Packard Children's Hospital Stanford (LPCH)
Palo Alto, California, 94304, United States
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National Center of Neurology and Psychiatry
Kodaira, Tokyo, 187-8551, Japan
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National Taiwan University Hospital
Taipei, 100225, Taiwan
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Nationwide Children's Hospital
Columbus, Ohio, 43205, United States
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Oregon Health and Science University
Portland, Oregon, 97239, United States
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Oxford University Hospitals NHS Foundation Trust
Oxford, Oxfordshire, OX3 9DU, United Kingdom
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Rady Children's Hospital
San Diego, California, 92123, United States
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The Johns Hopkins Hospital, Rubenstein Child Health Bldg
Baltimore, Maryland, 21287, United States
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Tokyo Women's Medical University Hospital
Tokyo, 1628666, Japan
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UCLA Medical Center
Los Angeles, California, 90095, United States
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UOC Neurologia Pediatrica e Malattie Muscolari, Istituto G. Gaslini, Istituto Pediatrico di Ricovero e Cura a Carattere Scientifico
Genova, 16147, Italy
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UOC Neurologia, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico
Milan, 20122, Italy
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UOC Neuropsichiatria Infantile, Area Salute del Bambino, Fondazione Policlinico Universitario A. Gemelli IRCCS, Universita Cattoclica del Sacro Cuore
Roma, 00168, Italy
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Universitair Ziekenhuis Gent, Neuromuscular Reference Centre (NMRC)
Ghent, East Flanders, 9000, Belgium
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University of California, Davis
Sacramento, California, 95817, United States
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University of Florida Clinical Research Center
Gainesville, Florida, 32610, United States
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University of Iowa ICTS Clinical Research Unit
Iowa City, Iowa, 52242, United States
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University of Rochester Medical Center
Rochester, New York, 14642, United States
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University of Utah Health
Salt Lake City, Utah, 84132, United States
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Universitätsklinikum Essen - Klinik für Kinderheilkunde I
Essen, North Rhine-Westphalia, 45147, Germany
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Washington University School of Medicine
St Louis, Missouri, 63110, United States
Conditions
Explore the condition pages connected to this study.