Extended trial tests CF drug's lasting power for rare mutations
NCT ID NCT05331183
Summary
This study follows 297 cystic fibrosis patients to see how safe and effective a triple-combination drug remains over the long term. The treatment targets specific genetic mutations beyond the most common one. Participants had previously taken the medication in earlier studies and are being monitored for lung function, symptoms, and side effects.
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Contacts and locations
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Locations
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Amsterdam UMC - locatie AMC - Afdeling Longgeneeskunde
Amsterdam, Netherlands
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Azienda Ospedaliera Regionale 'San Carlo', Potenza
Potenza, Italy
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Azienda Ospedaliera di Verona - Ospedale Civile Maggiore
Verona, Italy
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Azienda Ospedaliero Universitaria (AOU) San Luigi Gonzaga
Orbassano, Italy
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Azienda Ospedaliero Universitaria Federico II Napoli
Naples, Italy
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Azienda Ospedaliero Universitaria Ospedale Meyer
Florence, Italy
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Azienda Ospedaliero Universitaria delle Marche
Ancona, Italy
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British Columbia Children's Hospital
Vancouver, Canada
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CHU de Nice - Hôpital Pasteur 2
Nice, France
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CUB Hôpital Erasme
Brussels, Belgium
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Centre Hospitalier Intercommunal Creteil - Pulmonology
Créteil, France
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Centre de Perharidy, Roscoff
Roscoff, France
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Charité - Paediatric Pulmonology Department
Berlin, Germany
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Dr. von Haunersches Kinderspital - Pulmonology
München, Germany
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Erasmus Medisch Centrum - Pulmonology
Rotterdam, Netherlands
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Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico
Milan, Italy
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Fondazione IRCCS Ospedale Maggiore Policlinico, Mangiagalli e Regina Elena
Milan, Italy
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HagaZiekenhuis
The Hague, Netherlands
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Hopital Arnaud de Villeneuve - Service de Pneumologie et Maladies Respiratoires
Montpellier, France
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Hopital Bretonneau
Tours, France
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Hopital Cochin - Pulmonology
Paris, France
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Hopital Femme Mere-Enfant
Bron, France
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Hopital Larrey
Toulouse, France
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Hopital Necker Enfants Malades - Pulmonology
Paris, France
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Hopital Nord
Marseille, France
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Hopital Robert Debre - Pulmonology
Paris, France
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Hospital Infantil Universitario Nino Jesus
Madrid, Spain
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Hospital Saint Joan de Deu
Barcelona, Spain
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Hospital Universitari Vall d´Hebron Servicio de Broncoscopia
Barcelona, Spain
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Hospital Universitario 12 de Octubre - Pulmonology
Madrid, Spain
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Hospital Universitario Ramon y Cajal - Pulmonology
Madrid, Spain
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Hospital Universitario Virgen del Rocio
Seville, Spain
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Hospital Universitario de Jerez de la Frontera
Jerez de la Frontera, Spain
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Hospital Universitario y Politecnico La Fe - Pulmonology
Valencia, Spain
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Hospital Virgen de la Arrixaca
Murcia, Spain
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Hospital de Cruces
Barakaldo, Spain
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Hospital for Sick Children - Pulmonology
Toronto, Canada
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Hôpital Lyon Sud - Pulmonology
Pierre-Bénite, France
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Hôpital Nord Laennec
Nantes, France
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Hôpital Sud - Rennes
Rennes, France
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Hôpital américain de Reims - Département de pédiatrie A
Reims, France
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IRCCS Istituto Giannina Gaslini-Ospedale Pediatrico
Genova, Italy
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IRCSS Ospedale Pediatrico Bambino Gesu - Pulmonology
Rome, Italy
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Institut Cœur Poumon, CHU de Lille
Lille, France
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Institut d´Investigacio i Innovacio Parc Tauli
Sabadell, Spain
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Instytut Matki i Dziecka, Klinika Mukowiscydozy IMiD, Oddział Chorób Płuc SZPZOZ im.Dzieci Warszawy w Dziekanowie Leśnym
Łomianki, Poland
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Johannes Gutenberg-Universitaet
Mainz, Germany
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Justus-Liebig-Universität Gießen
Giessen, Germany
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Karolinska University Hospital - Pulmonology
Stockholm, Sweden
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Kinderspital Zuerich
Zurich, Switzerland
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Klinik für Kinder- und Jugendmedizin
Münster, Germany
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Klinika Detskych Infekcnich Nemoci
Brno, Czechia
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Klinikum Westbrandenburg (CF)
Potsdam, Germany
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Klinikum der Johann-Wolfgang-Goethe Universitaet - Pulmonology
Frankfurt, Germany
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La Paz Infantil
Madrid, Spain
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Le Centre de recherche du CHUM (CRCHUM)
Montreal, Canada
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Lungenheilkunde Munchen - Pasing
München, Germany
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McGill University Health Centre, Glen Site, Montreal Children's Hospital
Montreal, Canada
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Medizinische Hochschule Hannover
Hanover, Germany
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Medizinische Hochschule Hannover - Clinic for Pediatric Pneumology, Allergology and Neonatology, CF-Centre
Hanover, Germany
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Medizinische Universität Innsbruck - Heilstättenschule Universitätsklinik
Innsbruck, Austria
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Motol University Hospital
Prague, Czechia
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Mukoviszidose-Zentrum am Universitätsklinikum Jena
Jena, Germany
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National Koranyi Institute for TBC and Pulmonology
Budapest, Hungary
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Oslo University Hospital, Department of Paediatric Medicine
Oslo, Norway
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Pediatric Hospital Polanki named of Maciej Płażyński
Gdansk, Poland
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Policlinico Universitario G. Martino
Messina, Italy
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Radboud University Medical Center - Pulmonology
Nijmegen, Netherlands
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Ruhrlandklinik
Essen, Germany
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Sahlgrenska Universitetssjukhuset - Göteborg CF-center
Gothenburg, Sweden
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St. Paul's Hospital - Pulmonology
Vancouver, Canada
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Stollery Children's Hospital
Edmonton, Canada
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UMCU, Locatie Wilhelmina Kinderziekenhuis
Utrecht, Netherlands
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UZ Brussel - Campus Jette
Brussels, Belgium
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Unidade Local de Saúde de Santa Maria, E.P.E. - Pulmonology
Lisbon, Portugal
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Universitair Ziekenhuis Antwerpen (UZA) - Antwerp University Hospital
Edegem, Belgium
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Universitair Ziekenhuis Gent
Ghent, Belgium
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Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg
Leuven, Belgium
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Universite Catholique de Louvain - Pulmonology
Woluwe-Saint-Lambert, Belgium
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University Hospital Cologne (Koeln) - CF-Studienzentrum
Cologne, Germany
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Universitätsklinikum Halle (Saale) / Universitätsklinik und Poliklinik für Innere Medizin, Schwerpunkt Pneumologie
Halle, Germany
Conditions
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