Extended trial tests CF drug's lasting power for rare mutations

NCT ID NCT05331183

Summary

This study follows 297 cystic fibrosis patients to see how safe and effective a triple-combination drug remains over the long term. The treatment targets specific genetic mutations beyond the most common one. Participants had previously taken the medication in earlier studies and are being monitored for lung function, symptoms, and side effects.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Amsterdam UMC - locatie AMC - Afdeling Longgeneeskunde

    Amsterdam, Netherlands

  • Azienda Ospedaliera Regionale 'San Carlo', Potenza

    Potenza, Italy

  • Azienda Ospedaliera di Verona - Ospedale Civile Maggiore

    Verona, Italy

  • Azienda Ospedaliero Universitaria (AOU) San Luigi Gonzaga

    Orbassano, Italy

  • Azienda Ospedaliero Universitaria Federico II Napoli

    Naples, Italy

  • Azienda Ospedaliero Universitaria Ospedale Meyer

    Florence, Italy

  • Azienda Ospedaliero Universitaria delle Marche

    Ancona, Italy

  • British Columbia Children's Hospital

    Vancouver, Canada

  • CHU de Nice - Hôpital Pasteur 2

    Nice, France

  • CUB Hôpital Erasme

    Brussels, Belgium

  • Centre Hospitalier Intercommunal Creteil - Pulmonology

    Créteil, France

  • Centre de Perharidy, Roscoff

    Roscoff, France

  • Charité - Paediatric Pulmonology Department

    Berlin, Germany

  • Dr. von Haunersches Kinderspital - Pulmonology

    München, Germany

  • Erasmus Medisch Centrum - Pulmonology

    Rotterdam, Netherlands

  • Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

    Milan, Italy

  • Fondazione IRCCS Ospedale Maggiore Policlinico, Mangiagalli e Regina Elena

    Milan, Italy

  • HagaZiekenhuis

    The Hague, Netherlands

  • Hopital Arnaud de Villeneuve - Service de Pneumologie et Maladies Respiratoires

    Montpellier, France

  • Hopital Bretonneau

    Tours, France

  • Hopital Cochin - Pulmonology

    Paris, France

  • Hopital Femme Mere-Enfant

    Bron, France

  • Hopital Larrey

    Toulouse, France

  • Hopital Necker Enfants Malades - Pulmonology

    Paris, France

  • Hopital Nord

    Marseille, France

  • Hopital Robert Debre - Pulmonology

    Paris, France

  • Hospital Infantil Universitario Nino Jesus

    Madrid, Spain

  • Hospital Saint Joan de Deu

    Barcelona, Spain

  • Hospital Universitari Vall d´Hebron Servicio de Broncoscopia

    Barcelona, Spain

  • Hospital Universitario 12 de Octubre - Pulmonology

    Madrid, Spain

  • Hospital Universitario Ramon y Cajal - Pulmonology

    Madrid, Spain

  • Hospital Universitario Virgen del Rocio

    Seville, Spain

  • Hospital Universitario de Jerez de la Frontera

    Jerez de la Frontera, Spain

  • Hospital Universitario y Politecnico La Fe - Pulmonology

    Valencia, Spain

  • Hospital Virgen de la Arrixaca

    Murcia, Spain

  • Hospital de Cruces

    Barakaldo, Spain

  • Hospital for Sick Children - Pulmonology

    Toronto, Canada

  • Hôpital Lyon Sud - Pulmonology

    Pierre-Bénite, France

  • Hôpital Nord Laennec

    Nantes, France

  • Hôpital Sud - Rennes

    Rennes, France

  • Hôpital américain de Reims - Département de pédiatrie A

    Reims, France

  • IRCCS Istituto Giannina Gaslini-Ospedale Pediatrico

    Genova, Italy

  • IRCSS Ospedale Pediatrico Bambino Gesu - Pulmonology

    Rome, Italy

  • Institut Cœur Poumon, CHU de Lille

    Lille, France

  • Institut d´Investigacio i Innovacio Parc Tauli

    Sabadell, Spain

  • Instytut Matki i Dziecka, Klinika Mukowiscydozy IMiD, Oddział Chorób Płuc SZPZOZ im.Dzieci Warszawy w Dziekanowie Leśnym

    Łomianki, Poland

  • Johannes Gutenberg-Universitaet

    Mainz, Germany

  • Justus-Liebig-Universität Gießen

    Giessen, Germany

  • Karolinska University Hospital - Pulmonology

    Stockholm, Sweden

  • Kinderspital Zuerich

    Zurich, Switzerland

  • Klinik für Kinder- und Jugendmedizin

    Münster, Germany

  • Klinika Detskych Infekcnich Nemoci

    Brno, Czechia

  • Klinikum Westbrandenburg (CF)

    Potsdam, Germany

  • Klinikum der Johann-Wolfgang-Goethe Universitaet - Pulmonology

    Frankfurt, Germany

  • La Paz Infantil

    Madrid, Spain

  • Le Centre de recherche du CHUM (CRCHUM)

    Montreal, Canada

  • Lungenheilkunde Munchen - Pasing

    München, Germany

  • McGill University Health Centre, Glen Site, Montreal Children's Hospital

    Montreal, Canada

  • Medizinische Hochschule Hannover

    Hanover, Germany

  • Medizinische Hochschule Hannover - Clinic for Pediatric Pneumology, Allergology and Neonatology, CF-Centre

    Hanover, Germany

  • Medizinische Universität Innsbruck - Heilstättenschule Universitätsklinik

    Innsbruck, Austria

  • Motol University Hospital

    Prague, Czechia

  • Mukoviszidose-Zentrum am Universitätsklinikum Jena

    Jena, Germany

  • National Koranyi Institute for TBC and Pulmonology

    Budapest, Hungary

  • Oslo University Hospital, Department of Paediatric Medicine

    Oslo, Norway

  • Pediatric Hospital Polanki named of Maciej Płażyński

    Gdansk, Poland

  • Policlinico Universitario G. Martino

    Messina, Italy

  • Radboud University Medical Center - Pulmonology

    Nijmegen, Netherlands

  • Ruhrlandklinik

    Essen, Germany

  • Sahlgrenska Universitetssjukhuset - Göteborg CF-center

    Gothenburg, Sweden

  • St. Paul's Hospital - Pulmonology

    Vancouver, Canada

  • Stollery Children's Hospital

    Edmonton, Canada

  • UMCU, Locatie Wilhelmina Kinderziekenhuis

    Utrecht, Netherlands

  • UZ Brussel - Campus Jette

    Brussels, Belgium

  • Unidade Local de Saúde de Santa Maria, E.P.E. - Pulmonology

    Lisbon, Portugal

  • Universitair Ziekenhuis Antwerpen (UZA) - Antwerp University Hospital

    Edegem, Belgium

  • Universitair Ziekenhuis Gent

    Ghent, Belgium

  • Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg

    Leuven, Belgium

  • Universite Catholique de Louvain - Pulmonology

    Woluwe-Saint-Lambert, Belgium

  • University Hospital Cologne (Koeln) - CF-Studienzentrum

    Cologne, Germany

  • Universitätsklinikum Halle (Saale) / Universitätsklinik und Poliklinik für Innere Medizin, Schwerpunkt Pneumologie

    Halle, Germany

Conditions

Explore the condition pages connected to this study.