Major trial tests long-term safety of new cystic fibrosis treatment
NCT ID NCT05444257
Summary
This study is testing the long-term safety and effectiveness of a three-drug combination therapy (VX-121/TEZ/D-IVA) for people with cystic fibrosis. It follows 822 participants who previously completed earlier studies of this treatment. The main goals are to monitor side effects over time and see how well the treatment continues to work on lung function and other CF symptoms.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Aarhus University Hospital
Aarhus, Denmark
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Academisch Medisch Centrum (Academic Medical Centre)
Amsterdam, Netherlands
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Akron Children's Hospital
Akron, Ohio, 44308, United States
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Albany Medical College, Pulmonary and Critical Care Medicine
Albany, New York, 12208, United States
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Alfred Hospital
Melbourne, Australia
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All Wales Adult Cystic Fibrosis Centre, University Hospital Llandough
Penarth, United Kingdom
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Atrium Health Levine Children's Hospital
Charlotte, North Carolina, 28207, United States
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Augusta University
Augusta, Georgia, 30912, United States
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Azienda Ospedaliera di Verona - Ospedale Civile Maggiore
Verona, Italy
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Azienda Ospedaliero Universitaria Ospedale Pediatrico Meyer
Florence, Italy
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Azienda Ospedaliero Universitaria Ospedale Riuniti
Ancona, Italy
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Banner University of Arizona Medical Center
Tucson, Arizona, 85724, United States
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Billings Clinic
Billings, Montana, 59101, United States
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Birmingham Heartlands Hospital
Birmingham, United Kingdom
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Boston Children's Hospital
Boston, Massachusetts, 02115, United States
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British Columbia Children's Hospital
Vancouver, Canada
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CF Therapeutics Development Center of Western New York
Buffalo, New York, 14203, United States
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CHP - Hospital de Santo Antonio
Porto, Portugal
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CHU Lyon - Hopital Femme Mere-Enfant
Bron, France
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CHU de Rouen - Hopital Charles Nicolle
Rouen, France
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Canterbury District Health Board
Christchurch, New Zealand
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Cardinal Glennon Children's Hospital - St. Louis University
St Louis, Missouri, 63104, United States
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Central Florida Pulmonary Group,PA
Orlando, Florida, 32803, United States
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Centre Hospitalier Intercommunal Creteil
Créteil, France
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Centre Hospitalier Lyon Sud
Pierre-Bénite, France
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Centre Hospitalier Universitaire (CHU) de Nice - Hopital Pasteur
Nice, France
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Centre Hospitalier de l'Universite de Montreal (CHUM) Hotel-Dieu
Montreal, Canada
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Centre de Perharidy
Roscoff, France
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Centro Regionale Fibrosi Cistica, A.O. Ospedale San Carlo
Potenza, Italy
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Charite Paediatric Pulmonology Department
Berlin, Germany
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Children's Health Ireland at Crumlin
Dublin, Ireland
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Children's Health Ireland at Temple Street
Dublin, Ireland
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Children's Hospital Los Angeles
Los Angeles, California, 90027, United States
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Children's Hospital of Colorado
Aurora, Colorado, 80045, United States
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Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
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Childrens Hospital University of Missouri Health Sciences Center
Columbia, Missouri, 65212, United States
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Clinical Research Facility
Newcastle upon Tyne, United Kingdom
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Clinical Research Facility, Queen Elizabeth University Hospital
Glasgow, United Kingdom
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Cliniques Universitaires Saint-Luc
Woluwe-Saint-Lambert, Belgium
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Cliniques Universitaires de Bruxelles Hopital Erasme
Brussels, Belgium
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Columbia University Medical Center
New York, New York, 10032, United States
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Cook Children's Health Care System
Fort Worth, Texas, 76104, United States
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Cork University Hospital
Cork, Ireland
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Corporacio Sanitaria Parc Tauli - Sabadell Hospital Universitari
Sabadell, Spain
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Dartmouth Hitchcock
Manchester, New Hampshire, 03104, United States
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Dayton Children's Hospital
Dayton, Ohio, 45404, United States
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Erasmus Medical Center
Rotterdam, Netherlands
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Fakultni nemocnice v Motole
Prague, Czechia
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Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico
Milan, Italy
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Fondazione IRCCS Ospedale Maggiore Policlinico, Mangiagalli e Regina Elena
Milan, Italy
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Friedrich-Alexander University of Erlangen-Nuremberg, University Children's Hospital
Erlangen, Germany
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General Hospital of Thessaloniki "Papanikolaou"
Thessaloniki, Greece
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General Hospital of Thessaloniki 'Hippokratio', 3rd Pediatrics Department of Aristotle University of Thessaloniki
Thessaloniki, Greece
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Greenlane Clinical Centre
One Tree Hill, New Zealand
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Groupe Hospitaler Pellegrin, CHU De Bordeaux
Bordeaux, France
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Hadassah Medical Organization
Jerusalem, Israel
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HagaZiekenhuis van den Haag
The Hague, Netherlands
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Hannover Medical School
Hanover, Germany
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Harper University Hospital
Detroit, Michigan, 48201, United States
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Haukeland Universitetssjukehus (CF)
Bergen, Norway
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Hopital Arnaud de Villeneuve
Montpellier, France
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Hopital Bretonneau
Tours, France
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Hopital Cochin
Paris, France
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Hopital Foch (Suresnes), Hopital Foch, Adultes
Suresnes, France
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Hopital Robert Debre
Paris, France
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Hospital Saint Joan de Deu
Barcelona, Spain
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Hospital Sao Joao
Porto, Portugal
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Hospital Universitari Vall d'Hebron
Barcelona, Spain
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Hospital Universitario 12 de Octubre
Madrid, Spain
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Hospital Universitario Ramon y Cajal
Madrid, Spain
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Hospital Universitario Virgen del Rocio
Seville, Spain
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Hospital Universitario y Politecnico La Fe
Valencia, Spain
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Hospital Virgen de la Arrixaca
Murcia, Spain
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Hospital de Santa Maria
Lisbon, Portugal
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Hôpital de Hautepierre, AX5
Strasbourg, France
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IRCCS Istituto Giannina Gaslini-Ospedale Pediatrico
Genova, Italy
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Indiana University
Indianapolis, Indiana, 46202, United States
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Institut Cœur Poumon, CHU de Lille
Lille, France
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Institut Universitaire de Cardiologie et Pneumologie de Quebec - Universite Laval
Québec, Canada
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Institute for Respiratory Health
Nedlands, Australia
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Joe DiMaggio Cystic Fibrosis & Pulmonary Center
Hollywood, Florida, 33021, United States
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Johann Wolfgang Goethe University
Frankfurt, Germany
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Johannes Gutenberg-Universitaet
Mainz, Germany
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Johns Hopkins All Children's Hospital Outpatient Care Center
St. Petersburg, Florida, 33701, United States
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Juliane Marie Center, Rigshospitalet
Copenhagen, Denmark
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Justus-Liebig-Universität Gießen Zentrum für Kinderheilkunde und Jugendmedizin
Giessen, Germany
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Kaiser Permanente
Oakland, California, 94611, United States
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Karolinska Universitetssjukhuset, Huddinge
Stockholm, Sweden
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Kinderklinik III, Abt. fur Pneumologie
Essen, Germany
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Kinderspital Zuerich
Zurich, Switzerland
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King's College Hospital
London, United Kingdom
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Klinika Detskych Infekcnich Nemoci
Brno, Czechia
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Klinika Mukowiscydozy IMD Oddozial Chorob Pluc Szpzoz IM. Dzieci WarszaWY
Łomianki, Poland
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Klinikum Westbrandenburg (CF)
Potsdam, Germany
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Leeds General Infirmary
Leeds, United Kingdom
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Liverpool Heart and Chest Hospital
Liverpool, United Kingdom
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Long Island Jewish Medical Center
New Hyde Park, New York, 11040, United States
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Lund University Skanes Universitetssjukhus
Lund, Sweden
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Maine Medical Partners
Portland, Maine, 04102, United States
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Malattie Apparato Respiratorio 2 - Centro Fibrosi Cistica
Orbassano, Italy
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Massachusetts General Hospital Cystic Fibrosis Center Clinical Research Center
Boston, Massachusetts, 02114, United States
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Mater Adult Hospital
South Brisbane, Australia
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McGill University Health Centre, Glen Site, Montreal Children's Hospital
Montreal, Canada
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Medizinische Hochschule Hannover
Hanover, Germany
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Medizinische Universität Innsbruck
Innsbruck, Austria
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Medizinische Universität Wien
Vienna, Austria
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Michigan Medicine
Ann Arbor, Michigan, 48109, United States
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Miller Children's Hospital / Long Beach Memorial
Long Beach, California, 90806, United States
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Morristown Medical Center
Morristown, New Jersey, 07960, United States
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Mukoviszidose-Zentrum am Universitätsklinikum Jena, Klinik für Kinder- und Jugendmedizin
Jena, Germany
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National Jewish Health
Denver, Colorado, 80206, United States
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National Koranyi Institute for TBC and Pulmonology
Budapest, Hungary
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Nationwide Children's Hospital
Columbus, Ohio, 43205, United States
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Nebraska Medical Center
Omaha, Nebraska, 68198, United States
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Nemours Children's Specialty Care
Pensacola, Florida, 32514, United States
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New York Medical College
Valhalla, New York, 10595, United States
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Northwestern Memorial Hospital
Chicago, Illinois, 60611, United States
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Oregon Health & Science University
Portland, Oregon, 97239, United States
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Oslo University Hospital, Department of Paediatric Medicine
Oslo, Norway
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Pediatric Hospital Polanki named of Maciej Płażyński
Gdansk, Poland
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Pneumologisches Studienzentrum Muenchen-West
München, Germany
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Prisma Health Richland Campus
Columbia, South Carolina, 29203, United States
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ProMedica Toledo Hospital/Toledo Children's Hospital/Pediatric Pulmonary & Cystic Fibrosis Center
Toledo, Ohio, 43606, United States
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Providence Pediatric Pulmonary & Cystic Fibrosis Clinic
Spokane, Washington, 99204, United States
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Pulmonology Institute Torokbalint
Törökbálint, Hungary
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Queensland Children's Hospital
South Brisbane, Australia
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Riley Hospital for Children at Indiana University Health
Indianapolis, Indiana, 46202, United States
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Royal Brompton Hospital
London, United Kingdom
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Royal Devon University Healthcare NHS Foundation Trust
Exeter, United Kingdom
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Royal Manchester Children's Hospital
Manchester, United Kingdom
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Royal Papworth Hospital NHS Foundation Trust
Cambridge, United Kingdom
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Royal Prince Alfred Hospital
Camperdown, Australia
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Ruhrlandklinik Westdeutsches Lungenzentrum am Klinikum Essen
Essen, Germany
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SUNY Upstate Medical University
Syracuse, New York, 13210, United States
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Sahlgrenska Universitetssjukhuset
Gothenburg, Sweden
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Sanford Children's Speciality Clinic
Sioux Falls, South Dakota, 57105, United States
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Santiago Reyes, M.D.
Oklahoma City, Oklahoma, 73112, United States
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Schneider Children's Medical Center of Israel
Petach Tikvah, Israel
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Sheba Medical Center - The Edmond and Lili Safra Children's Hospital
Tel Litwinsky, Israel
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Southampton General Hospital
Southampton, United Kingdom
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Spectrum Health Medical Group Adult Cystic Fibrosis Care Center
Grand Rapids, Michigan, 49546, United States
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St. Bartholomew's Hospital
London, United Kingdom
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St. James University Hospital
Leeds, United Kingdom
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St. Joseph's Health Care London
London, Canada
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St. Luke's Cystic Fibrosis Center of Idaho
Boise, Idaho, 83702, United States
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St. Paul's Hospital
Vancouver, Canada
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St. Vincent's University Hospital
Dublin, Ireland
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Starship Children's Hospital
Grafton, New Zealand
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Stollery Children's Hospital
Edmonton, Canada
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Telethon Kids Institute
Nedlands, Australia
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Texas Children's Hospital - Baylor College of Medicine
Houston, Texas, 77030, United States
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The Children's Mercy Hospital
Kansas City, Missouri, 64108, United States
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The Emory Clinic at Chantilly
Atlanta, Georgia, 30324, United States
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The Prince Charles Hospital
Chermside, Australia
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The Royal Children's Hospital
Parkville, Australia
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The University of Texas Southwestern Medical Center
Dallas, Texas, 75390, United States
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Tulane Medical Center
New Orleans, Louisiana, 70112, United States
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UMC St. Radboud
Nijmegen, Netherlands
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UMass Memorial Medical Center
Worcester, Massachusetts, 01655, United States
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UPMC Children's Hospital of Pittsburgh
Pittsburgh, Pennsylvania, 15224, United States
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Uniklinikum Salzburg - Universitätsklinik für Pneumologie/Lungenheilkunde
Salzburg, Austria
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Universitair Ziekenhuis Brussel - Campus Jette
Brussels, Belgium
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Universitair Ziekenhuis Gent
Ghent, Belgium
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Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg
Leuven, Belgium
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University Hospital Limerick (Pediatrics)
Limerick, Ireland
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University Hospital and UW Health Clinics
Madison, Wisconsin, 53792, United States
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University Hospitals Bristol and Weston NHS Foundation Trust, Bristol Royal Hospital
Bristol, United Kingdom
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University Medical Center, Utrecht, Department of Pulmonology and Tuberculosis
Utrecht, Netherlands
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University of Alabama at Birmingham
Birmingham, Alabama, 35233, United States
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University of Arkansas for Medical Sciences
Little Rock, Arkansas, 72205, United States
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University of Calgary Medical Clinic of the Foothills Medical Centre
Calgary, Canada
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University of California Davis Medical Center
Sacramento, California, 95817, United States
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University of California San Francisco, Lung Transplant Program
San Francisco, California, 94143, United States
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University of Florida, Shands Hospital
Gainesville, Florida, 32610, United States
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University of Graz
Graz, Austria
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University of Kansas Medical Center
Kansas City, Kansas, 66160, United States
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University of Kentucky
Lexington, Kentucky, 40508, United States
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University of Miami Miller School of Medicine
Miami, Florida, 33136, United States
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University of Minnesota
Minneapolis, Minnesota, 55455, United States
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University of Oklahoma Health Sciences Center
Oklahoma City, Oklahoma, 73104, United States
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University of Tennessee Medical Center
Knoxville, Tennessee, 37920, United States
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University of Utah
Salt Lake City, Utah, 84132, United States
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University of Virginia Health System
Charlottesville, Virginia, 22908, United States
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University of Washington Medical Center
Seattle, Washington, 98195, United States
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Universitätsklinikum Ulm, Klinik für Kinder- und Jugendmedizin (CF)
Ulm, Germany
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Universitätsklinikum Würzburg
Würzburg, Germany
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Vanderbilt University Medical Center, Nephrology Clinical Trials Center
Nashville, Tennessee, 37232, United States
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Vermont Lung Center
Colchester, Vermont, 05446, United States
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Waikato Hospital
Hamilton, New Zealand
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Wake Forest Baptist Health
Winston-Salem, North Carolina, 27104, United States
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Washington University School of Medicine / St. Louis Children's Hospital
St Louis, Missouri, 63110, United States
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West Virginia University
Morgantown, West Virginia, 26506, United States
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Western General Hospital
Edinburgh, United Kingdom
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Westmead Hospital
Westmead, Australia
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Wythenshawe Hospital
Manchester, United Kingdom
Conditions
Explore the condition pages connected to this study.