Muscular dystrophy patients continue experimental treatment in Long-Term safety study
NCT ID NCT06066580
Summary
This study continues testing an experimental drug called sevasemten (EDG-5506) in people with Becker muscular dystrophy to see how safe it is over the long term. It's open to 260 adults and adolescents who have already participated in earlier studies of this same medication. Researchers will monitor side effects and check if the drug continues to help with muscle function over an extended period.
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Contacts and locations
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Locations
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AP-HP Hopital Pitie-Salpetriere
Paris, France, 75013, France
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Arkansas Children's Hospital
Little Rock, Arkansas, 72202, United States
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Azienda Ospedale - Università Padova
Padua, Italy, 35128, Italy
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CHU de Nantes
Nantes, France, 44093, France
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CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies Neuromusculaires
Nice, France, 06001, France
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Centre Hospitalier Régional de la Citadelle
Liége, Belgium, 4000, Belgium
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Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La Timone
Marseille, France, 13005, France
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Fondazione IRCCS Ca'Granda Ospedale Maggiore
Milan, Italy, 20122, Italy
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Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore
Rome, Italy, 00168, Italy
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Hadassah University Hospital
Jerusalem, 91240, Israel
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Hospital Universitari i Politecnic La Fe
Valencia, Spain, 46026, Spain
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Hospital Universitario Donostia
Donostia / San Sebastian, Spain, 20014, Spain
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Hospital Universitario Vall d'Hebron
Barcelona, Spain, 08035, Spain
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Hospital Universitario de Bellvitge
Barcelona, Spain, 08907, Spain
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Indiana University School of Medicine
Indianapolis, Indiana, 46202, United States
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Kennedy Krieger Institute
Baltimore, Maryland, 21205, United States
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Klinikum der Ludwig-Maximilians-Universitaet Muenchen
Munich, Germany, 80336, Germany
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Leids Universitair Medisch Centrum
Leiden, 2333 ZA, Netherlands
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National Neuromuscular Research Institute
Austin, Texas, 78759, United States
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Nationwide Children's Hospital
Columbus, Ohio, 43205, United States
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Neurology Rare Disease Center
Denton, Texas, 76208, United States
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Newcastle Freeman Hospital
Newcastle, NE7 7DN, United Kingdom
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Northwestern University
Chicago, Illinois, 60611, United States
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Rare Disease Research
Atlanta, Georgia, 30329, United States
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Rare Disease Research, LLC NC
Hillsborough, North Carolina, 27278, United States
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Rigshospitalet
Copenhagen, 2100, Denmark
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Salford Royal Hospital
Salford, United Kingdom, M68HD, United Kingdom
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St. George's University Hospitals NHS Foundation Trust
London, SW17 0QT, United Kingdom
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Stanford Neuroscience Health Center
Palo Alto, California, 94304, United States
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UC Davis Medical Center
Sacramento, California, 95817, United States
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UC Denver
Aurora, Colorado, 80045, United States
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UC Irvine Medical Center
Orange, California, 92868, United States
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UC San Diego
La Jolla, California, 92037, United States
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UCLA Medical Center
Los Angeles, California, 90095, United States
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Universitaire Ziekenhuizen Leuven
Leuven, Belgium, 3000, Belgium
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University College London Hospital
London, NW1 2PG, United Kingdom
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University Hospital Gent
Ghent, Belgium, 9000, Belgium
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University of Cincinnati Gardner Neuroscience Institute
Cincinnati, Ohio, 45219, United States
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University of Florida
Gainesville, Florida, 32611, United States
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University of Iowa
Iowa City, Iowa, 52242, United States
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University of Kansas Medical Center
Kansas City, Kansas, 66160, United States
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University of Massachusetts Memorial Medical Center
Worcester, Massachusetts, 01605, United States
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University of Pennsylvania
Philadelphia, Pennsylvania, 19104, United States
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University of Rochester Medical Center
Rochester, New York, 14642, United States
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Virginia Commonwealth University Health
Richmond, Virginia, 23298, United States
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Washington University School of Medicine
St Louis, Missouri, 63110, United States
Conditions
Explore the condition pages connected to this study.