Researchers track hidden liver risks in rare muscle disease
NCT ID NCT06581146
Summary
This study aims to understand how often liver problems occur in boys with X-linked myotubular myopathy (XLMTM), a serious genetic muscle condition. It will follow about 50 boys under 18 for one year, checking their liver health with scans every 6 weeks. The study only collects health information; it does not test any new treatments.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Ann & Robert H. Lurie Children's Hospital of Chicago
RECRUITINGChicago, Illinois, 60611, United States
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Boston Children's Hospital
RECRUITINGBoston, Massachusetts, 02115, United States
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Children's Hospital of Philadelphia
RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
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Cincinnati Children's Hospital Medical Center
RECRUITINGCincinnati, Ohio, 45229, United States
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UPMC Children's Hospital of Pittsburgh
RECRUITINGPittsburgh, Pennsylvania, 15224, United States
Conditions
Explore the condition pages connected to this study.