Study withdrawn before launch: planned research to map rare muscle disease

NCT ID NCT06210672

Summary

This study aimed to track how a rare genetic muscle disease (LGMDR5) changes over two years in patients aged 6 to 35. It planned to measure walking, arm function, breathing, and muscle health to better understand the disease. The goal was to gather information to help design future treatment trials, but the study was withdrawn before any participants were enrolled.

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Contacts and locations

Locations

  • Hedi Chaker Hospital Child Neurology Department

    Sfax, Tunisia

  • Hopital Raymond Poincare

    Garches, 92380, France

  • National Institute Mongi Ben Hmida of Neurology

    Tunis, Tunisia

Conditions

Explore the condition pages connected to this study.