New gene therapy aims to reduce bleeding in hemophilia a

NCT ID NCT03217032

First seen May 10, 2026 · Last updated May 14, 2026 · Updated 1 time

Summary

This early-stage trial tests a gene therapy that delivers a working copy of the clotting factor VIII gene into the blood cells of people with hemophilia A. The goal is to see if it is safe and can reduce bleeding episodes. The study involves 10 male participants aged 2 and older with severe hemophilia A.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Shenzhen Geno-immune Medical Institute

    RECRUITING

    Shenzhen, Guangdong, 518000, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.