New hope for kids with rare leukemia as experimental treatment begins testing

NCT ID NCT05849662

First seen Apr 17, 2026 · Last updated Apr 17, 2026

Summary

This study is testing whether combining two drugs, trametinib and azacitidine, is safe and effective for children with juvenile myelomonocytic leukemia (JMML), a rare and aggressive blood cancer. Children with lower-risk JMML will receive just the two drugs, while those with higher-risk disease will also receive additional chemotherapy. The trial aims to find better treatment options for this serious childhood cancer.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • C.S. Mott Children's Hospital

    RECRUITING

    Ann Arbor, Michigan, 48109, United States

    Contact

  • Children's Hospital Los Angeles

    RECRUITING

    Los Angeles, California, 900027, United States

    Contact

  • Children's Hospital of Atlanta

    RECRUITING

    Atlanta, Georgia, 30322, United States

    Contact

  • Children's Hospital of Colorado

    RECRUITING

    Denver, Colorado, 80045, United States

    Contact

  • Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

    Contact

  • Children's Mercy Hospital

    RECRUITING

    Kansas City, Missouri, 64108, United States

    Contact

  • Children's National Medical Center

    RECRUITING

    Washington D.C., District of Columbia, 20010, United States

    Contact

  • Cincinnati Children's Hospital Medical Center

    RECRUITING

    Cincinnati, Ohio, 45229, United States

    Contact

  • Indiana University/Riley Hospital for Children

    RECRUITING

    Indianapolis, Indiana, 46202, United States

    Contact

  • Lurie Children's Hospital of Chicago

    RECRUITING

    Chicago, Illinois, 60611, United States

    Contact

  • Memorial Sloan Kettering Cancer Center

    RECRUITING

    New York, New York, 10065, United States

    Contact

  • Oregon Health & Science University

    RECRUITING

    Portland, Oregon, 97239, United States

    Contact

  • Phoenix Children's Hospital

    RECRUITING

    Phoenix, Arizona, 85016, United States

    Contact

  • Primary Children's Hospital

    RECRUITING

    Salt Lake City, Utah, 84113, United States

    Contact

  • Seattle Children's Hospital

    RECRUITING

    Seattle, Washington, 98105, United States

    Contact

  • Sidney Kimmel Cancer Center at Johns Hopkins

    RECRUITING

    Baltimore, Maryland, 21231, United States

    Contact

  • St. Jude Children's Research Hospital Memphis

    RECRUITING

    Memphis, Tennessee, 38105, United States

    Contact

  • University of California San Francisco

    RECRUITING

    San Francisco, California, 94158, United States

    Contact

  • University of Miami

    RECRUITING

    Miami, Florida, 33136, United States

    Contact

Conditions

Explore the condition pages connected to this study.