Real-World study of iptacopan for PNH in russia ends early

NCT ID NCT07036718

First seen Dec 08, 2025 · Last updated May 07, 2026 · Updated 26 times

Summary

This study followed 6 adults with paroxysmal nocturnal hemoglobinuria (PNH) who were already taking iptacopan as part of their routine care in Russia. The goal was to see if the drug helped raise hemoglobin levels and reduce the need for blood transfusions over 6 to 12 months. The study was terminated early, so results are limited.

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Contacts and locations

Locations

  • Novartis Investigative Site

    Syktyvkar, Komi, 167904, Russia

  • Novartis Investigative Site

    Grozny, 364047, Russia

  • Novartis Investigative Site

    Moscow, 129110, Russia

  • Novartis Investigative Site

    Murmansk, 183047, Russia

  • Novartis Investigative Site

    Yuzhno-Sakhalinsk, 693000, Russia

Conditions

Explore the condition pages connected to this study.