New drug study aims to transform care for rare blood disorder

NCT ID NCT06931691

Summary

This study is observing how a drug called iptacopan affects adults in China with a rare blood disease called paroxysmal nocturnal hemoglobinuria (PNH). It will follow 80 patients who are starting this new treatment to see if it improves their blood counts, reduces symptoms, and changes how much medical care they need. The goal is to understand the real-world benefits and management of this condition with the new medication.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

Locations

  • Novartis Investigative Site

    RECRUITING

    Guangzhou, Guangdong, 510000, China

  • Novartis Investigative Site

    RECRUITING

    Shijiazhuang, Hebei, 050000, China

  • Novartis Investigative Site

    RECRUITING

    Zhengzhou, Henan, 450008, China

  • Novartis Investigative Site

    RECRUITING

    Wuhan, Hubei, 430030, China

  • Novartis Investigative Site

    RECRUITING

    Nanchang, Jiangxi, 330006, China

  • Novartis Investigative Site

    RECRUITING

    Changchun, Jilin, 130021, China

  • Novartis Investigative Site

    RECRUITING

    Tianjin, 300020, China

  • Novartis Investigative Site

    RECRUITING

    Tianjin, 300052, China

  • Novartis Investigative Site

    RECRUITING

    Wuhan, 430022, China

Conditions

Explore the condition pages connected to this study.