Spinal injection trial offers new hope for angelman syndrome
NCT ID NCT05127226
Summary
This study is testing a new drug called ION582 for Angelman syndrome, a rare genetic disorder. The drug is given as an injection into the spinal fluid. The main goals are to see if it's safe and how the body processes it in about 70 participants, including children under 2 years old.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for ANGELMAN SYNDROME are added.
By submitting, you agree to our Terms of use
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
By submitting, you agree to our Terms of use
Study contacts
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
-
Azienda Ospedaliera Universitaria Pisana
RECRUITINGPisa, 56126, Italy
-
Boston Children's Hospital
RECRUITINGBoston, Massachusetts, 02215, United States
-
Colorado Children's Hospital Research Institute
RECRUITINGAurora, Colorado, 80045, United States
-
Necker-Enfants Malades Hospital
RECRUITINGParis, 75015, France
-
Rady Children's Hospital
RECRUITINGSan Diego, California, 92123, United States
-
Rush University Medical Center
RECRUITINGChicago, Illinois, 60612, United States
-
STRONG Group University of Oxford
ACTIVE_NOT_RECRUITINGOxford, Oxfordshire, OX3 9DU, United Kingdom
-
Sheba Medical Center
RECRUITINGRamat Gan, 5262100, Israel
-
Sydney Children's Hospital, Kids Cancer Centre
ACTIVE_NOT_RECRUITINGRandwick, NSW 2031, Australia
-
Texas Children's Hospital
ACTIVE_NOT_RECRUITINGHouston, Texas, 77030, United States
-
University of North Carolina at Chapel Hill School of Medicine
RECRUITINGCarrboro, North Carolina, 27510, United States
Conditions
Explore the condition pages connected to this study.