New drug trial aims to protect kids from inherited heart risk
NCT ID NCT06597019
Summary
This study is testing a drug called inclisiran to see if it safely lowers bad cholesterol in children aged 6 to 12 who have an inherited condition causing very high cholesterol. For the first year, some children will receive the drug and others a placebo, followed by a year where all children receive the drug. The goal is to control this lifelong condition early to help prevent future heart problems.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
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Children's National Hospital
NOT_YET_RECRUITINGWashington D.C., District of Columbia, 20010, United States
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Childrens National Hospital
RECRUITINGWashington D.C., District of Columbia, 20010, United States
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Excel Medical Clinical Trials LLC
RECRUITINGBoca Raton, Florida, 33434, United States
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Icahn School of Med at Mt Sinai
RECRUITINGNew York, New York, 10029, United States
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Novartis Investigative Site
RECRUITINGBuenos Aires, C1245AAM, Argentina
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Novartis Investigative Site
RECRUITINGCABA, C1181ACH, Argentina
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Novartis Investigative Site
RECRUITINGSalzburg, 5020, Austria
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Novartis Investigative Site
RECRUITINGVienna, 1090, Austria
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Novartis Investigative Site
RECRUITINGBrussels, 1200, Belgium
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Novartis Investigative Site
RECRUITINGLeuven, 3000, Belgium
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Novartis Investigative Site
RECRUITINGFortaleza, Ceará, 60430-275, Brazil
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Novartis Investigative Site
RECRUITINGRio de Janeiro, Rio de Janeiro, 20211-340, Brazil
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Novartis Investigative Site
RECRUITINGPorto Alegre, Rio Grande do Sul, 90020-020, Brazil
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Novartis Investigative Site
RECRUITINGSão Paulo, São Paulo, 05403 000, Brazil
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Novartis Investigative Site
RECRUITINGBeijing, Beijing Municipality, 100013, China
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Novartis Investigative Site
RECRUITINGShanghai, 200127, China
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Novartis Investigative Site
RECRUITINGPrague, 128 08, Czechia
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Novartis Investigative Site
RECRUITINGPrague, 150 06, Czechia
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Novartis Investigative Site
RECRUITINGMarseille, 13885, France
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Novartis Investigative Site
RECRUITINGNantes, 44093, France
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Novartis Investigative Site
RECRUITINGParis, 75012, France
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Novartis Investigative Site
RECRUITINGFreiburg im Breisgau, Baden-Wurttemberg, 79106, Germany
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Novartis Investigative Site
RECRUITINGFrankfurt am Main, Hesse, 60590, Germany
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Novartis Investigative Site
RECRUITINGHanover, 30173, Germany
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Novartis Investigative Site
RECRUITINGAthens, 115 27, Greece
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Novartis Investigative Site
RECRUITINGIoannina, 455 00, Greece
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Novartis Investigative Site
RECRUITINGHong Kong, 999077, Hong Kong
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Novartis Investigative Site
RECRUITINGBudapest, 1026, Hungary
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Novartis Investigative Site
RECRUITINGJerusalem, 9112001, Israel
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Novartis Investigative Site
RECRUITINGRamat Gan, 5265601, Israel
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Novartis Investigative Site
RECRUITINGMilan, MI, 20162, Italy
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Novartis Investigative Site
RECRUITINGRoma, RM, 00165, Italy
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Novartis Investigative Site
RECRUITINGTorino, TO, 10126, Italy
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Novartis Investigative Site
RECRUITINGVerona, VR, 3712, Italy
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Novartis Investigative Site
RECRUITINGKuala Lumpur, Kuala Lumpur, 50586, Malaysia
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Novartis Investigative Site
RECRUITINGAmsterdam, North Holland, 1105 AZ, Netherlands
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Novartis Investigative Site
RECRUITINGBialystok, 15-274, Poland
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Novartis Investigative Site
RECRUITINGGdansk, 80 952, Poland
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Novartis Investigative Site
RECRUITINGLodz, Łódź Voivodeship, 93-338, Poland
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Novartis Investigative Site
RECRUITINGCoimbra, 3000-602, Portugal
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Novartis Investigative Site
RECRUITINGLisbon, 1649-035, Portugal
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Novartis Investigative Site
RECRUITINGPorto, 4050-651, Portugal
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Novartis Investigative Site
RECRUITINGPorto, 4200 319, Portugal
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Novartis Investigative Site
RECRUITINGBloemfontein, Free State, 9301, South Africa
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Novartis Investigative Site
RECRUITINGElche, Alicante, 03203, Spain
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Novartis Investigative Site
RECRUITINGCadiz, Andalusia, 11009, Spain
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Novartis Investigative Site
RECRUITINGEsplugues, Barcelona, 08950, Spain
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Novartis Investigative Site
RECRUITINGBadalona, Catalonia, 08916, Spain
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Novartis Investigative Site
RECRUITINGPamplona, Navarre, 31008, Spain
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Novartis Investigative Site
RECRUITINGBarcelona, 08041, Spain
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Novartis Investigative Site
RECRUITINGMálaga, 29011, Spain
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Novartis Investigative Site
RECRUITINGSeville, 41013, Spain
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Novartis Investigative Site
RECRUITINGTaipei, 111045, Taiwan
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Novartis Investigative Site
RECRUITINGTaipei, 11217, Taiwan
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Novartis Investigative Site
RECRUITINGAdana, Saricam, 01330, Turkey (Türkiye)
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Novartis Investigative Site
RECRUITINGAnkara, Yenimahalle, 06500, Turkey (Türkiye)
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Novartis Investigative Site
RECRUITINGIzmir, 35100, Turkey (Türkiye)
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Novartis Investigative Site
RECRUITINGWest Midlands, Birmingham, B4 6NH, United Kingdom
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Novartis Investigative Site
RECRUITINGLondon, NW3 2QG, United Kingdom
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Primary Childrens Medical Center
NOT_YET_RECRUITINGSalt Lake City, Utah, 84113, United States
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Primary Childrens Medical Center
RECRUITINGSalt Lake City, Utah, 84113, United States
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UC San Francisco Medical Center
RECRUITINGSan Francisco, California, 94143, United States
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UC San Francisco Medical Center
RECRUITINGSan Francisco, California, 94143, United States
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Virginia Commonwealth University
RECRUITINGRichmond, Virginia, 23298, United States
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West Virginia Childrens Hospital
RECRUITINGMorgantown, West Virginia, 26506, United States
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West Virginia Childrens Hospital
RECRUITINGMorgantown, West Virginia, 26506, United States
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Contact Phone: •••-•••-•••• Email: •••••@•••••
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Conditions
Explore the condition pages connected to this study.