New drug tested to protect teens from severe genetic heart risk

NCT ID NCT04659863

Summary

This study tested a drug called inclisiran in teenagers (ages 12-17) with a rare, severe genetic condition that causes very high cholesterol from birth. The goal was to see if the drug was safe and effective at lowering 'bad' cholesterol (LDL-C) when added to their current standard treatments. For the first year, some participants received the drug and others received a placebo, and then all received the drug in the second year.

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Contacts and locations

Locations

  • American University of Beirut Medical Center

    Beirut, 1107 2020, Lebanon

  • Excel Medical Clinical Trials LLC

    Boca Raton, Florida, 33434, United States

  • Hotel Dieu de France Hospital

    El Achrafiyé, 166830, Lebanon

  • Metropolitan Hospital

    Athens, 18547, Greece

  • Novartis Investigative Site

    Québec, Quebec, G1V 4W2, Canada

  • Novartis Investigative Site

    Bron, 69677, France

  • Novartis Investigative Site

    Kuala Lumpur, 59100, Malaysia

  • Novartis Investigative Site

    Amsterdam, 1105 AZ, Netherlands

  • Novartis Investigative Site

    Istanbul, TUR, 34098, Turkey (Türkiye)

  • Novartis Investigative Site

    Izmir, 35100, Turkey (Türkiye)

  • University General Hospital of Ioannina

    Ioannina, GR, 455 00, Greece

Conditions

Explore the condition pages connected to this study.