Can a common arthritis drug make PKU therapy safer and more effective?

NCT ID NCT07477691

First seen Mar 18, 2026 · Last updated May 13, 2026 · Updated 8 times

Summary

This study tests whether adding methotrexate (a drug that calms the immune system) can help adults with PKU tolerate and respond better to Palynziq, a treatment that lowers harmful phenylalanine levels. About 12 adults will receive both drugs for 6 months, and researchers will measure blood Phe levels and immune markers. The goal is to reduce allergic-type reactions and improve long-term disease control.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Ann & Robert H. Lurie Children's Hospital of Chicago

    Chicago, Illinois, 60611, United States

  • Children's Hospital Colorado

    Aurora, Colorado, 80045, United States

  • Children's Hospital of Wisconsin

    Milwaukee, Wisconsin, 53226, United States

  • Indiana University School of Medicine

    Indianapolis, Indiana, 46202, United States

  • Oregon Health & Science University (OHSU) - PARENT

    Portland, Oregon, 97239, United States

  • UCLA Dept. of Human Genetics

    Los Angeles, California, 90095, United States

  • UT Southwestern Medical Center

    Dallas, Texas, 75390, United States

    Contact

  • University Of South Florida Medical Center

    Tampa, Florida, 33613, United States

  • University of Minnesota Medical School

    Minneapolis, Minnesota, 55455, United States

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh

    Philadelphia, Pennsylvania, 19104, United States

  • University of Rochester Medical Center (URMC)

    Rochester, New York, 14642, United States

  • University of Utah Hospital

    Salt Lake City, Utah, 84108, United States

Conditions

Explore the condition pages connected to this study.