Global study tracks rare bone disease over time

NCT ID NCT02306720

ENROLLING_BY_INVITATION Knowledge-focused Sponsor: Alexion Pharmaceuticals, Inc. Source: ClinicalTrials.gov ↗

Summary

This study is creating a long-term registry to better understand hypophosphatasia (HPP), a rare genetic bone disorder. It will follow over 1,500 patients of all ages worldwide to track how the disease progresses naturally and how it affects daily life. The registry will also monitor the long-term safety and effectiveness of the treatment asfotase alfa for those who receive it.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

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Locations

Leicester Royal Infirmary

Leicester, Leicestershire, LE1 5WW, United Kingdom
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Centennial, Colorado, 80112, United States
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Hartford, Connecticut, 06106, United States
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Tampa, Florida, 33606, United States
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Decatur, Georgia, 30033, United States
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Baltimore, Maryland, 21287, United States
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Boston, Massachusetts, 02111, United States
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Boston, Massachusetts, 02115, United States
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Minneapolis, Minnesota, 55454, United States
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Kansas City, Missouri, 64108, United States
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St Louis, Missouri, 63110, United States
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Hackensack, New Jersey, 07601, United States
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Mineola, New York, 11501, United States
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Durham, North Carolina, 27710, United States
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Cincinnati, Ohio, 45229, United States
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Columbus, Ohio, 43205, United States
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Pittsburgh, Pennsylvania, 15224, United States
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Nashville, Tennessee, 37212, United States
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Salt Lake City, Utah, 84112, United States
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Charlottesville, Virginia, 22903, United States
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Madison, Wisconsin, 53792, United States
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Clayton, Victoria, Australia
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Parkville, Victoria, Australia
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Herston, Australia
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South Brisbane, Australia
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Linz, Austria
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Winnipeg, Manitoba, Canada
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Oakville, Ontario, Canada
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Ottawa, Ontario, Canada
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Toronto, Ontario, M5G 2C4, Canada
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Toulouse, Haute Garonne, France
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Lille, Nord, France
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Paris, Paris, France
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Poitiers, Vienne, France
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Lyon, France
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Paris, France
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Le Kremlin-Bicêtre, Île-de-France Region, France
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Bad Reichenhall, Bavaria, Germany
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Würzburg, Bavaria, Germany
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Bochum, North Rhine-Westphalia, Germany
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Düsseldorf, North Rhine-Westphalia, Germany
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Dresden, Saxony, Germany
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Berlin, Germany
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Cologne, Germany
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Giessen, Germany
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Homburg, Germany
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Mainz, Germany
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Milan, Milano, 20132, Italy
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Florence, Italy
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Pisa, Italy
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Rome, Italy
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San Giovanni Rotondo, Italy
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Lodz, Poland
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Warsaw, Poland
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Riyadh, Saudi Arabia
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Madrid, Spain
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Bristol, Avon, United Kingdom
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London, Greater London, United Kingdom
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Stanmore, Middlesex, United Kingdom
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Oxford, Oxfordshire, United Kingdom
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Sheffield, South Yorkshire, United Kingdom
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Newcastle upon Tyne, Tyne & Wear, United Kingdom
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Birmingham, West Midlands, United Kingdom
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Belfast, United Kingdom

Conditions

Explore the condition pages connected to this study.

HYPOPHOSPHATASIA (HPP)