Scientists build database to unlock mysteries of rare childhood neurological disease

NCT ID NCT04712812

Summary

This study aims to gather detailed health information and biological samples from children and young adults (under 30) with early-onset hereditary spastic paraplegia (HSP), a group of rare genetic disorders that cause progressive stiffness and weakness in the legs. By tracking participants over time and creating a registry, researchers hope to better understand how the disease develops, identify targets for future therapies, and help design better clinical trials. The study does not test a treatment but seeks to build the knowledge needed for future breakthroughs.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Email: •••••@•••••

Locations

  • Boston Children's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

    Contact Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.